Improving outcome measures in late onset Pompe disease: Modified Rasch-Built Pompe-Specific Activity scale
改善晚发型庞贝病结局指标:改良的Rasch构建庞贝特异性活动量表
期刊:European Journal of Neurology
影响因子:3.9
doi:10.1111/ene.16397
van Kooten, Harmke A; Horton, Mike C; Wenninger, Stephan; Babačić, Haris; Schoser, Benedikt; Lefeuvre, Claire; Taouagh, Najib; Laforêt, Pascal; Segovia, Sonia; Díaz-Manera, Jordi; Claeys, Kristl G; Mongini, Tiziana; Musumeci, Olimpia; Toscano, Antonio; Hundsberger, Thomas; Brusse, Esther; van Doorn, Pieter A; van der Ploeg, Ans T; van der Beek, Nadine A M E