日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Barcoded Hybrids of Extracellular Vesicles and Lipid Nanoparticles for Multiplexed Analysis of Tissue Distribution

细胞外囊泡和脂质纳米颗粒的条形码混合物用于组织分布的多重分析

Alena Ivanova, Renata Chalupska, Ana Filipa Louro, Mike Firth, Hernán González-King Garibotti, Leif Hultin, Franziska Kohl, Elisa Lázaro-Ibáñez, Julia Lindgren, Gentian Musa, Erik Oude Blenke, Andreia M Silva, Louis Szeponik, Agnes Taylor, Ida Viken, Xiaoqin Wang, Karin Jennbacken, John Wiseman, Nie

Epigenetic modulators link mitochondrial redox homeostasis to cardiac function in a sex-dependent manner

表观遗传调节剂以性别依赖的方式将线粒体氧化还原稳态与心脏功能联系起来

Zaher ElBeck, Mohammad Bakhtiar Hossain, Humam Siga, Nikolay Oskolkov, Fredrik Karlsson, Julia Lindgren, Anna Walentinsson, Dominique Koppenhöfer, Rebecca Jarvis, Roland Bürli, Tanguy Jamier, Elske Franssen, Mike Firth, Andrea Degasperi, Claus Bendtsen, Robert I Menzies, Katrin Streckfuss-Bömeke, Mi

An aptamer-mediated base editing platform for simultaneous knockin and multiple gene knockout for allogeneic CAR-T cells generation

一种用于同种异体CAR-T细胞生成的适体介导的碱基编辑平台,可同时实现基因敲入和多基因敲除。

Immacolata Porreca ,Robert Blassberg ,Jennifer Harbottle ,Bronwyn Joubert ,Olga Mielczarek ,Jesse Stombaugh ,Kevin Hemphill ,Jonathan Sumner ,Deividas Pazeraitis ,Julia Liz Touza ,Margherita Francescatto ,Mike Firth ,Tommaso Selmi ,Juan Carlos Collantes ,Zaklina Strezoska ,Benjamin Taylor ,Shengkan Jin ,Ceri M Wiggins ,Anja van Brabant Smith ,John J Lambourne

In vivo phage display identifies novel peptides for cardiac targeting

体内噬菌体展示鉴定出用于心脏靶向的新型肽

Alena Ivanova, Franziska Kohl, Hernán González-King Garibotti, Renata Chalupska, Aleksander Cvjetkovic, Mike Firth, Karin Jennbacken, Sofia Martinsson, Andreia M Silva, Ida Viken, Qing-Dong Wang, John Wiseman, Niek Dekker

Outcomes in people with eating disorders: a transdiagnostic and disorder-specific systematic review, meta-analysis and multivariable meta-regression analysis

进食障碍患者的预后:一项跨诊断和特定障碍的系统评价、荟萃分析和多变量荟萃回归分析

Solmi, Marco; Monaco, Francesco; Højlund, Mikkel; Monteleone, Alessio M; Trott, Mike; Firth, Joseph; Carfagno, Marco; Eaton, Melissa; De Toffol, Marco; Vergine, Mariantonietta; Meneguzzo, Paolo; Collantoni, Enrico; Gallicchio, Davide; Stubbs, Brendon; Girardi, Anna; Busetto, Paolo; Favaro, Angela; Carvalho, Andre F; Steinhausen, Hans-Christoph; Correll, Christoph U

A Type II-B Cas9 nuclease with minimized off-targets and reduced chromosomal translocations in vivo

II-B 型 Cas9 核酸酶,可最大程度减少脱靶并减少体内染色体易位

Burcu Bestas, Sandra Wimberger #, Dmitrii Degtev #, Alexandra Madsen, Antje K Rottner, Fredrik Karlsson, Sergey Naumenko, Megan Callahan, Julia Liz Touza, Margherita Francescatto, Carl Ivar Möller, Lukas Badertscher, Songyuan Li, Silvia Cerboni, Niklas Selfjord, Elke Ericson, Euan Gordon, Mike Firth

Simultaneous inhibition of DNA-PK and Polϴ improves integration efficiency and precision of genome editing

同时抑制DNA-PK和Polϴ提高基因组编辑的整合效率和精度

Sandra Wimberger, Nina Akrap, Mike Firth, Johan Brengdahl, Susanna Engberg, Marie K Schwinn, Michael R Slater, Anders Lundin, Pei-Pei Hsieh, Songyuan Li, Silvia Cerboni, Jonathan Sumner, Burcu Bestas, Bastian Schiffthaler, Björn Magnusson, Silvio Di Castro, Preeti Iyer, Mohammad Bohlooly-Y, Thomas M

Engineered Cas9 extracellular vesicles as a novel gene editing tool

工程化 Cas9 细胞外囊泡作为一种新型基因编辑工具

Xabier Osteikoetxea, Andreia Silva, Elisa Lázaro-Ibáñez, Nikki Salmond, Olga Shatnyeva, Josia Stein, Jan Schick, Stephen Wren, Julia Lindgren, Mike Firth, Alexandra Madsen, Lorenz M Mayr, Ross Overman, Rick Davies, Niek Dekker

Universal toxin-based selection for precise genome engineering in human cells

基于通用毒素的选择,实现人类细胞的精准基因组工程

Songyuan Li, Nina Akrap #, Silvia Cerboni #, Michelle J Porritt, Sandra Wimberger, Anders Lundin, Carl Möller, Mike Firth, Euan Gordon, Bojana Lazovic, Aleksandra Sieńska, Luna Simona Pane, Matthew A Coelho, Giovanni Ciotta, Giovanni Pellegrini, Marcella Sini, Xiufeng Xu, Suman Mitra, Mohammad Bohlo

Correction of a urea cycle defect after ex vivo gene editing of human hepatocytes

人类肝细胞体外基因编辑后尿素循环缺陷的纠正

Mihaela Zabulica, Raghuraman C Srinivasan, Pinar Akcakaya, Gabriella Allegri, Burcu Bestas, Mike Firth, Christina Hammarstedt, Tomas Jakobsson, Towe Jakobsson, Ewa Ellis, Carl Jorns, Georgios Makris, Tanja Scherer, Nicole Rimann, Natalie R van Zuydam, Roberto Gramignoli, Anna Forslöw, Susanna Engber