Antisense oligonucleotide treatment rescues UBE3A expression and multiple phenotypes of an Angelman syndrome mouse model
反义寡核苷酸治疗可挽救Angelman综合征小鼠模型中的UBE3A表达和多种表型
期刊:JCI Insight
影响因子:6.1
doi:10.1172/jci.insight.145991
Milazzo, Claudia; Mientjes, Edwin J; Wallaard, Ilse; Rasmussen, Søren Vestergaard; Erichsen, Kamille Dumong; Kakunuri, Tejaswini; van der Sman, A S Elise; Kremer, Thomas; Miller, Meghan T; Hoener, Marius C; Elgersma, Ype
