日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Engineering altered protein-DNA recognition specificity

工程改造蛋白质-DNA识别特异性

Bogdanove, Adam J; Bohm, Andrew; Miller, Jeffrey C; Morgan, Richard D; Stoddard, Barry L

Toward eliminating HLA class I expression to generate universal cells from allogeneic donors

旨在消除HLA I类分子的表达,从而从同种异体供体中生成通用细胞

Torikai, Hiroki; Reik, Andreas; Soldner, Frank; Warren, Edus H; Yuen, Carrie; Zhou, Yuanyue; Crossland, Denise L; Huls, Helen; Littman, Nicholas; Zhang, Ziying; Tykodi, Scott S; Kebriaei, Partow; Lee, Dean A; Miller, Jeffrey C; Rebar, Edward J; Holmes, Michael C; Jaenisch, Rudolf; Champlin, Richard E; Gregory, Philip D; Cooper, Laurence J N

A foundation for universal T-cell based immunotherapy: T cells engineered to express a CD19-specific chimeric-antigen-receptor and eliminate expression of endogenous TCR

基于T细胞的通用免疫疗法的基础:经基因工程改造的T细胞,使其表达CD19特异性嵌合抗原受体并消除内源性TCR的表达。

Torikai, Hiroki; Reik, Andreas; Liu, Pei-Qi; Zhou, Yuanyue; Zhang, Ling; Maiti, Sourindra; Huls, Helen; Miller, Jeffrey C; Kebriaei, Partow; Rabinovich, Brian; Lee, Dean A; Champlin, Richard E; Bonini, Chiara; Naldini, Luigi; Rebar, Edward J; Gregory, Philip D; Holmes, Michael C; Cooper, Laurence J N

Genetic engineering of human pluripotent cells using TALE nucleases

利用TALE核酸酶对人类多能干细胞进行基因工程改造

Hockemeyer, Dirk; Wang, Haoyi; Kiani, Samira; Lai, Christine S; Gao, Qing; Cassady, John P; Cost, Gregory J; Zhang, Lei; Santiago, Yolanda; Miller, Jeffrey C; Zeitler, Bryan; Cherone, Jennifer M; Meng, Xiangdong; Hinkley, Sarah J; Rebar, Edward J; Gregory, Philip D; Urnov, Fyodor D; Jaenisch, Rudolf

Efficient targeted gene disruption in the soma and germ line of the frog Xenopus tropicalis using engineered zinc-finger nucleases.

利用工程化锌指核酸酶对非洲爪蟾的体细胞和生殖细胞进行高效的靶向基因破坏

Young John J, Cherone Jennifer M, Doyon Yannick, Ankoudinova Irina, Faraji Farhoud M, Lee Andrew H, Ngo Catherine, Guschin Dmitry Y, Paschon David E, Miller Jeffrey C, Zhang Lei, Rebar Edward J, Gregory Philip D, Urnov Fyodor D, Harland Richard M, Zeitler Bryan

Zinc-finger nuclease-driven targeted integration into mammalian genomes using donors with limited chromosomal homology

利用锌指核酸酶驱动的靶向整合,以染色体同源性有限的供体为模板,整合到哺乳动物基因组中。

Orlando, Salvatore J; Santiago, Yolanda; DeKelver, Russell C; Freyvert, Yevgeniy; Boydston, Elizabeth A; Moehle, Erica A; Choi, Vivian M; Gopalan, Sunita M; Lou, Jacqueline F; Li, James; Miller, Jeffrey C; Holmes, Michael C; Gregory, Philip D; Urnov, Fyodor D; Cost, Gregory J

Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome

利用锌指核酸酶驱动的转基因技术,在人类基因组的安全港位点进行同源基因组学、蛋白质组学和调控DNA分析

DeKelver, Russell C; Choi, Vivian M; Moehle, Erica A; Paschon, David E; Hockemeyer, Dirk; Meijsing, Sebastiaan H; Sancak, Yasemin; Cui, Xiaoxia; Steine, Eveline J; Miller, Jeffrey C; Tam, Phillip; Bartsevich, Victor V; Meng, Xiangdong; Rupniewski, Igor; Gopalan, Sunita M; Sun, Helena C; Pitz, Kathleen J; Rock, Jeremy M; Zhang, Lei; Davis, Gregory D; Rebar, Edward J; Cheeseman, Iain M; Yamamoto, Keith R; Sabatini, David M; Jaenisch, Rudolf; Gregory, Philip D; Urnov, Fyodor D

Knockout rats via embryo microinjection of zinc-finger nucleases

通过胚胎显微注射锌指核酸酶构建基因敲除大鼠

Geurts, Aron M; Cost, Gregory J; Freyvert, Yevgeniy; Zeitler, Bryan; Miller, Jeffrey C; Choi, Vivian M; Jenkins, Shirin S; Wood, Adam; Cui, Xiaoxia; Meng, Xiangdong; Vincent, Anna; Lam, Stephen; Michalkiewicz, Mieczyslaw; Schilling, Rebecca; Foeckler, Jamie; Kalloway, Shawn; Weiler, Hartmut; Ménoret, Séverine; Anegon, Ignacio; Davis, Gregory D; Zhang, Lei; Rebar, Edward J; Gregory, Philip D; Urnov, Fyodor D; Jacob, Howard J; Buelow, Roland

Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases

利用锌指核酸酶进行基因组编辑,在CD4+ T细胞中建立HIV-1抗性

Perez, Elena E; Wang, Jianbin; Miller, Jeffrey C; Jouvenot, Yann; Kim, Kenneth A; Liu, Olga; Wang, Nathaniel; Lee, Gary; Bartsevich, Victor V; Lee, Ya-Li; Guschin, Dmitry Y; Rupniewski, Igor; Waite, Adam J; Carpenito, Carmine; Carroll, Richard G; Orange, Jordan S; Urnov, Fyodor D; Rebar, Edward J; Ando, Dale; Gregory, Philip D; Riley, James L; Holmes, Michael C; June, Carl H