日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Concept CARs are picking up speed

概念车正在加速发展

Mansilla-Soto, Jorge; Milone, Michael C

Clinical advances in gene, cell, and RNA therapies

基因、细胞和RNA疗法的临床进展

Milone, Michael C; Mansilla-Soto, Jorge; Pardi, Norbert; George, Lindsey A; Byrne, Barry J; Herzog, Roland W

Quadruple adenine base-edited allogeneic CAR T cells outperform CRISPR/Cas9 nuclease-engineered T cells

经四重腺嘌呤碱基编辑的同种异体CAR-T细胞优于CRISPR/Cas9核酸酶工程化T细胞

Engel, Nils W; Steinfeld, Israel; Ryan, Daniel; Anupindi, Kusala; Kim, Samuel; Wellhausen, Nils; Chen, Linhui; Wilkins, Katherine; Baker, Daniel J; Rommel, Philipp C; Jarocha, Danuta; Gohil, Mercy; Zhang, Qian; Milone, Michael C; Fraietta, Joseph A; Davis, Megan; Young, Regina M; June, Carl H

New approach to busulfan dosing in infants and children based on a population pharmacokinetic analysis

基于群体药代动力学分析的婴幼儿布苏凡给药新方法

Balis, Frank M; Rieger, Elizabeth; Bunin, Nancy J; Gardiner, JoAnn; Shaw, Leslie M; Olson, Timothy S; Milone, Michael C

Viral vector-free generation of orthogonal IL-2-responsive CAR T cells through gene editing of IL-2 and its receptor

通过基因编辑IL-2及其受体,无需病毒载体即可生成正交IL-2反应性CAR T细胞

Zhang, Qian; Wu, Yihao; Yang, Jingyi; Zhou, Kevin; Manoharan, Eric Nigel Ebenezer Anand; Wentz, Tyra; Su, Leon; Yu, Alvin; Wang, Hong-Yi; Bruhn, Laurakay; Steinfeld, Israel; Gonzalez, Nicolas; Song, Edward Z; Zhang, Yunlin; Hresko, Morgan E; Ryan, Daniel E; Engel, Nils W; Nunez-Cruz, Selene; June, Carl H; Garcia, K Christopher; Milone, Michael C

Author Correction: Precision targeting of autoantigen-specific B cells in muscle-specific tyrosine kinase myasthenia gravis with chimeric autoantibody receptor T cells

作者更正:利用嵌合自身抗体受体T细胞精准靶向肌肉特异性酪氨酸激酶重症肌无力中的自身抗原特异性B细胞

Oh, Sangwook; Mao, Xuming; Manfredo-Vieira, Silvio; Lee, Jinmin; Patel, Darshil; Choi, Eun Jung; Alvarado, Andrea; Cottman-Thomas, Ebony; Maseda, Damian; Tsao, Patricia Y; Ellebrecht, Christoph T; Khella, Sami L; Richman, David P; O'Connor, Kevin C; Herzberg, Uri; Binder, Gwendolyn K; Milone, Michael C; Basu, Samik; Payne, Aimee S

Bendamustine lymphodepletion before axicabtagene ciloleucel is safe and associates with reduced inflammatory cytokines

在接受阿西卡巴吉尼西洛莱赛治疗前进行苯达莫司汀淋巴清除是安全的,并且与炎症细胞因子减少有关。

Ghilardi, Guido; Paruzzo, Luca; Svoboda, Jakub; Chong, Eise A; Shestov, Alexander A; Chen, Linhui; Cohen, Ivan J; Gabrielli, Giulia; Nasta, Sunita D; Porazzi, Patrizia; Landsburg, Daniel J; Gerson, James N; Carter, Jordan; Barta, Stefan K; Yelton, Rebecca; Pajarillo, Raymone; Patel, Vrutti; White, Griffin; Ballard, Hatcher J; Weber, Elizabeth; Napier, Ellen; Chong, Emeline R; Fraietta, Joseph A; Garfall, Alfred L; Porter, David L; Milone, Michael C; O'Connor, Roderick; Schuster, Stephen J; Ruella, Marco

Association of Urine Fentanyl Concentration With Severity of Opioid Withdrawal Among Patients Presenting to the Emergency Department

尿液芬太尼浓度与急诊科就诊患者阿片类药物戒断症状严重程度的相关性

Thakrar, Ashish P; Faude, Sophia; Perrone, Jeanmarie; Milone, Michael C; Lowenstein, Margaret; Snider, Christopher K; Spadaro, Anthony; Delgado, M Kit; Nelson, Lewis S; Kilaru, Austin S

Changes in Bone Marrow Tumor and Immune Cells Correlate with Durability of Remissions Following BCMA CAR T Therapy in Myeloma

骨髓肿瘤和免疫细胞的变化与骨髓瘤患者接受BCMA CAR-T疗法后缓解期的持久性相关

Dhodapkar, Kavita M; Cohen, Adam D; Kaushal, Akhilesh; Garfall, Alfred L; Manalo, Renee Julia; Carr, Allison R; McCachren, Samuel S; Stadtmauer, Edward A; Lacey, Simon F; Melenhorst, J Joseph; June, Carl H; Milone, Michael C; Dhodapkar, Madhav V

Engineering enhanced CAR T-cells for improved cancer therapy

工程改造增强型CAR-T细胞以改善癌症治疗

Milone, Michael C; Xu, Jie; Chen, Sai-Juan; Collins, McKensie A; Zhou, Jianfeng; Powell, Daniel J Jr; Melenhorst, J Joseph