日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of a selection assay for small guide RNAs that drive efficient site-directed RNA editing

开发一种用于筛选驱动高效定点RNA编辑的小向导RNA的检测方法

Diaz Quiroz, Juan Felipe; Ojha, Namrata; Shayhidin, Elnur E; De Silva, Dasuni; Dabney, Jesse; Lancaster, Amy; Coull, James; Milstein, Stuart; Fraley, Andrew W; Brown, Christopher R; Rosenthal, Joshua J C

An RNAi therapeutic targeting Tmprss6 decreases iron overload in Hfe(-/-) mice and ameliorates anemia and iron overload in murine β-thalassemia intermedia

靶向Tmprss6的RNAi疗法可降低Hfe(-/-)小鼠的铁过载,并改善小鼠β-地中海贫血中间型的贫血和铁过载。

Schmidt, Paul J; Toudjarska, Iva; Sendamarai, Anoop K; Racie, Tim; Milstein, Stuart; Bettencourt, Brian R; Hettinger, Julia; Bumcrot, David; Fleming, Mark D

Improving dendritic cell vaccine immunogenicity by silencing PD-1 ligands using siRNA-lipid nanoparticles combined with antigen mRNA electroporation.

利用siRNA-脂质纳米颗粒结合抗原mRNA电穿孔技术沉默PD-1配体,从而提高树突状细胞疫苗的免疫原性

Hobo Willemijn, Novobrantseva Tatiana I, Fredrix Hanny, Wong Jamie, Milstein Stuart, Epstein-Barash Hila, Liu Ju, Schaap Nicolaas, van der Voort Robbert, Dolstra Harry

Therapeutic siRNA silencing in inflammatory monocytes in mice

小鼠炎症单核细胞中的治疗性siRNA沉默

Leuschner, Florian; Dutta, Partha; Gorbatov, Rostic; Novobrantseva, Tatiana I; Donahoe, Jessica S; Courties, Gabriel; Lee, Kang Mi; Kim, James I; Markmann, James F; Marinelli, Brett; Panizzi, Peter; Lee, Won Woo; Iwamoto, Yoshiko; Milstein, Stuart; Epstein-Barash, Hila; Cantley, William; Wong, Jamie; Cortez-Retamozo, Virna; Newton, Andita; Love, Kevin; Libby, Peter; Pittet, Mikael J; Swirski, Filip K; Koteliansky, Victor; Langer, Robert; Weissleder, Ralph; Anderson, Daniel G; Nahrendorf, Matthias

'Edgetic' perturbation of a C. elegans BCL2 ortholog

秀丽隐杆线虫BCL2直系同源物的“边缘性”扰动

Dreze, Matija; Charloteaux, Benoit; Milstein, Stuart; Vidalain, Pierre-Olivier; Yildirim, Muhammed A; Zhong, Quan; Svrzikapa, Nenad; Romero, Viviana; Laloux, Géraldine; Brasseur, Robert; Vandenhaute, Jean; Boxem, Mike; Cusick, Michael E; Hill, David E; Vidal, Marc

Edgetic perturbation models of human inherited disorders

人类遗传疾病的边缘扰动模型

Zhong, Quan; Simonis, Nicolas; Li, Qian-Ru; Charloteaux, Benoit; Heuze, Fabien; Klitgord, Niels; Tam, Stanley; Yu, Haiyuan; Venkatesan, Kavitha; Mou, Danny; Swearingen, Venus; Yildirim, Muhammed A; Yan, Han; Dricot, Amélie; Szeto, David; Lin, Chenwei; Hao, Tong; Fan, Changyu; Milstein, Stuart; Dupuy, Denis; Brasseur, Robert; Hill, David E; Cusick, Michael E; Vidal, Marc

hORFeome v3.1: a resource of human open reading frames representing over 10,000 human genes

hORFeome v3.1:一个包含超过10,000个人类基因的人类开放阅读框资源

Lamesch, Philippe; Li, Ning; Milstein, Stuart; Fan, Changyu; Hao, Tong; Szabo, Gabor; Hu, Zhenjun; Venkatesan, Kavitha; Bethel, Graeme; Martin, Paul; Rogers, Jane; Lawlor, Stephanie; McLaren, Stuart; Dricot, Amélie; Borick, Heather; Cusick, Michael E; Vandenhaute, Jean; Dunham, Ian; Hill, David E; Vidal, Marc

C. elegans GLA-3 is a novel component of the MAP kinase MPK-1 signaling pathway required for germ cell survival

秀丽隐杆线虫GLA-3是MAP激酶MPK-1信号通路的一个新组分,该通路对生殖细胞存活至关重要。

Kritikou, Ekaterini A; Milstein, Stuart; Vidalain, Pierre-Olivier; Lettre, Guillaume; Bogan, Erica; Doukoumetzidis, Kimon; Gray, Phillip; Chappell, Thomas G; Vidal, Marc; Hengartner, Michael O