Precise progerin targeting using RfxCas13d: A therapeutic avenue for Hutchinson-Gilford progeria syndrome
利用 RfxCas13d 精准靶向早衰蛋白:治疗哈钦森-吉尔福德早衰综合征的新途径
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2025.06.017
Unbin Chae ,Hae-Jun Yang ,Hanseop Kim ,Seung Hwan Lee ,Dong Gil Lee ,Jeong Young Koo ,Seung-Min Ha ,Seo-Jong Bak ,Mina Joo ,Hyun Hee Nam ,Kyung-Seob Lim ,Philyong Kang ,Hee-Chang Son ,You Jeong An ,Young-Hyun Kim ,In-Sung Song ,Sang-Hee Lee ,Hae Rim Kim ,Sang-Mi Cho ,Eun-Kyoung Kim ,Ki-Hoan Nam ,Kyung-Sook Chung ,Jae-Yoon Kim ,Seon-Yeop Kim ,Seon-Kyu Kim ,Seon-Young Kim ,Dong-Seok Lee ,Jin-Man Kim ,Young-Ho Park ,Sun-Uk Kim