日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

First-in-human high dose AAV9 intrathecal gene therapy for paediatric CLN7 disease: a phase 1, open-label, single ascending dose, non-randomised clinical trial

首次人体高剂量AAV9鞘内基因疗法治疗儿童CLN7疾病:一项1期、开放标签、单次递增剂量、非随机临床试验

Greenberg, Benjamin M; Minassian, Berge; Messahel, Souad; Edgar, Veronica Bordes; Lowden, Andrea; Dahshi, Hamza; Nettesheim, Emily R; Nguyen, Hoang H; Hughes, Samuel; Muthukumar, Alagar R; Srinivasan, Kalayarasan; Iannaccone, Susan; Varadarajan, Ganapathy; Gray, Steven J; Kayani, Saima N

Lafora disease gene therapy: EPM2A but not EPM2B overexpression results in Lafora body formation.

Lafora病基因治疗:EPM2A而非EPM2B过度表达会导致Lafora小体的形成。

Alao Esther O, Sheibani Mehrnaz, Wu Jun, Marriam Ummay, Evans Doretha, Kasiri Sahba, Verma Mayank, Nitschke Silvia, Nitschke Felix, Gray Steven J, Mitra Sharmistha, Minassian Berge A

B and T cell responses to pre-erythrocytic R21/Matrix-M and blood-stage RH5.1/Matrix-M malaria vaccines in endemic settings.

在疟疾流行地区,B 细胞和 T 细胞对红细胞前 R21/Matrix-M 和血液期 RH5.1/Matrix-M 疟疾疫苗的反应。

Bundi Caroline K, Muñoz Olivia, Kibwana Elizabeth, Bellamy Duncan, Stockdale Lisa, Barrett Jordan R, McHugh Kirsty, Mtaka Ivanny, Kalinga Wilmina, Kimani Domtila, Nyamako Lydia, Keter Kelvias, Ogwang Rodney, Hill Adrian V S, Bejon Philip, Hamaluba Mainga, Silk Sarah E, Minassian Angela M, Draper Simon J, Olotu Ally I, Kapulu Melissa C, Ewer Katie J, Nielsen Carolyn M

THC induced similar physiological effects on HIV transgenic rats and their controls without affecting HIV-induced deficits in effortful motivation

THC对HIV转基因大鼠及其对照组产生了类似的生理效应,但并未影响HIV引起的努力动机缺陷。

Vemuri, Sunitha; Ayoub, Samantha M; Minassian, Arpi; Young, Jared W

The experience of professionals receiving patients with manifestations of traumatic dissociation: a qualitative study

专业人员接诊创伤性分离症状患者的经验:一项定性研究

Mezard, Elea; El Husseini, Mayssa'; Radjack, Rahmeth; Moro, Marie Rose; Minassian, Sevan

CUL1 variants cause severe neurodevelopmental disorders: Insights from human genetics and a zebrafish model of microcephaly

CUL1 变异导致严重的神经发育障碍:来自人类遗传学和斑马鱼小头畸形模型的启示

Xu, Haoling; Liu, Zhen; Hamdan, Fadi F; Wu, Shengnan; He, Mei; Wang, Dan; Pan, Hu; Hu, Juanli; Chen, Yiqiao; Michaud, Jacques L; Minassian, Berge A; Duan, Jing; Liao, Jianxiang; Su, Jinping; Hu, Sainan; Peng, Yin; Ye, Qinyong; Chen, Li

Virtual prototyping of non-invasive spinal cord electrical stimulation targeting upper limb motor function

针对上肢运动功能的非侵入性脊髓电刺激的虚拟原型设计

Alashqar, Abdallah; Brihmat, Nabila; Gemar, Vincent; Hu, Zhaoshun; Koh, Seong-Ryong; Diaz-Pier, Sandra; de Freitas, Roberto; Sasaki, Atsushi; Milosevic, Matija; Keesey, Rodolfo; Seáñez, Ismael; Neufeld, Esra; Cassoudesalle, Hélène; Hofstoetter, Ursula; Minassian, Karen; Wagner, Fabien; Rowald, Andreas

Development of clinical immunity to Plasmodium vivax following repeat controlled human malaria infection

反复控制性人类疟疾感染后,对间日疟原虫产生临床免疫力

Hou, Mimi M; Harding, Adam C; Barber, Natalie M; Kundu, Prasun; Bach, Florian A; Salkeld, Jo; Themistocleous, Yrene; Greenwood, Nicola M; Cho, Jee-Sun; Barrett, Jordan R; Nugent, Fay L; Rawlinson, Thomas A; Hodgson, Susanne H; Khozoee, Baktash; Mac Lochlainn, Dylan J; Cowan, Rachel E; Poulton, Ian D; Baker, Megan; Kingham, Lucy; Mitton, Celia H; Platt, Abigail; Lopez Ramon, Raquel; Ramos Lopez, Fernando; Thomas, Merin; Skinner, Katherine; Quinkert, Doris; Pipini, Dimitra; Lias, Amelia M; Bardelli, Martino; Edwards, Nick J; Donnellan, Francesca R; Biswas, Sumi; Rayner, Julian C; Nielsen, Carolyn M; Silk, Sarah E; Draper, Simon J; Nahrendorf, Wiebke; Spence, Philip J; Minassian, Angela M

S100A8/9-NLRP3-mediated chronic unresolved inflammation drives cardiac pathologies following invasive pneumococcal disease

S100A8/9-NLRP3介导的慢性未消退炎症驱动侵袭性肺炎球菌疾病后的心脏病变

Tousif, Sultan; Minassian, Daniel; He, Chao; Singh, Baldeep; Umbarkar, Prachi; Bhati, Arvind Singh; Mohasin, Mohammed; Erdmann, Nathan; Xie, Min; Sethu, Palaniappan; Orihuela, Carlos J; Lal, Hind

Plasmodium falciparum infection induces T cell tolerance that is associated with decreased disease severity upon re-infection

恶性疟原虫感染可诱导T细胞耐受,这与再次感染后疾病严重程度降低有关。

Diana Muñoz Sandoval #,Florian A Bach #,Alasdair Ivens,Adam C Harding,Natasha L Smith,Michalina Mazurczyk,Yrene Themistocleous,Nick J Edwards,Sarah E Silk,Jordan R Barrett,Graeme J M Cowan,Giorgio Napolitani,Nicholas J Savill,Simon J Draper,Angela M Minassian,Wiebke Nahrendorf #,Philip J Spence #