日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A myotropic AAV vector combined with skeletal muscle cis-regulatory elements improve glycogen clearance in mouse models of Pompe disease.

肌营养性 AAV 载体与骨骼肌顺式调控元件相结合,可改善庞贝氏症小鼠模型中的糖原清除

Sellier P, Collaud F, Benchekroun Y Krimi, Jimenez V, Leon X, Daniele N, Pham Q H, El Andari J, VandenDriessche T, Chuah M K, Grimm D, Bosch F, Mingozzi F, Ronzitti G

Exosome-associated AAV vector as a robust and convenient neuroscience tool

外泌体相关腺相关病毒载体作为一种强大而便捷的神经科学工具

Hudry, E; Martin, C; Gandhi, S; György, B; Scheffer, D I; Mu, D; Merkel, S F; Mingozzi, F; Fitzpatrick, Z; Dimant, H; Masek, M; Ragan, T; Tan, S; Brisson, A R; Ramirez, S H; Hyman, B T; Maguire, C A