Extracellular Vesicles Administered via Intrathecal Injection Mediate Safe Delivery of Nucleic Acids to the Central Nervous System for Gene Therapy.
通过鞘内注射给药的细胞外囊泡可安全地将核酸输送到中枢神经系统进行基因治疗
期刊:Journal of Extracellular Vesicles
影响因子:14.5
doi:10.1002/jev2.70116
Lam Brenda Wan Shing, Tan Melissa, Gao Chang, Pham Thach Tuan, Tran Lan Thi Ngoc, Nguyen Lan Ngoc, Sidik Harwin, Lim Matthias B H, Le Anh Hong, Nguyen Tram T T, Lim Nicole, Nguyen Lap, Nguyen Thuy Huong, Loh Yuin-Han, Usman Muhammad Waqas, Le Minh T N