Long-term natural history in type II and III spinal muscular atrophy: a 4-year international study on the Hammersmith Functional Motor Scale Expanded
II型和III型脊髓性肌萎缩症的长期自然病程:一项为期4年的Hammersmith功能运动量表扩展版国际研究
期刊:European Journal of Neurology
影响因子:3.9
doi:10.1111/ene.16517
Coratti, Giorgia; Bovis, Francesca; Pera, Maria Carmela; Civitello, Matthew; Rohwer, Annemarie; Salmin, Francesca; Glanzman, Allan M; Montes, Jacqueline; Pasternak, Amy; De Sanctis, Roberto; Dunaway Young, Sally; Duong, Tina; Mizzoni, Irene; Milev, Evelin; Sframeli, Maria; Morando, Simone; Albamonte, Emilio; D'Amico, Adele; Catteruccia, Michela; Brolatti, Noemi; Pane, Marika; Scoto, Mariacristina; Messina, Sonia; Escudero, Jesica Exposito; De Waele, Liesbeth; Hirano, Michio; Zolkipli-Cunningham, Zarazuela; Darras, Basil T; Bertini, Enrico; Nascimiento Osorio, Andres; Bruno, Claudio; Goemans, Natalie; Sansone, Valeria A; Day, John; Baranello, Giovanni; Muntoni, Francesco; Finkel, Richard; Mercuri, Eugenio