日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Correction: Clinical Efficacy of ONC201 in H3K27M-Mutant Diffuse Midline Gliomas Is Driven by Disruption of Integrated Metabolic and Epigenetic Pathways

更正:ONC201治疗H3K27M突变型弥漫性中线胶质瘤的临床疗效是由整合代谢和表观遗传通路紊乱驱动的

Venneti, Sriram; Kawakibi, Abed Rahman; Ji, Sunjong; Waszak, Sebastian M; Sweha, Stefan R; Mota, Mateus; Pun, Matthew; Deogharkar, Akash; Chung, Chan; Tarapore, Rohinton S; Ramage, Samuel; Chi, Andrew; Wen, Patrick Y; Arrillaga-Romany, Isabel; Batchelor, Tracy T; Butowski, Nicholas A; Sumrall, Ashley; Shonka, Nicole; Harrison, Rebecca A; de Groot, John; Mehta, Minesh; Hall, Matthew D; Daghistani, Doured; Cloughesy, Timothy F; Ellingson, Benjamin M; Beccaria, Kevin; Varlet, Pascale; Kim, Michelle M; Umemura, Yoshie; Garton, Hugh; Franson, Andrea; Schwartz, Jonathan; Jain, Rajan; Kachman, Maureen; Baum, Heidi; Burant, Charles F; Mottl, Sophie L; Cartaxo, Rodrigo T; John, Vishal; Messinger, Dana; Qin, Tingting; Peterson, Erik; Sajjakulnukit, Peter; Ravi, Karthik; Waugh, Alyssa; Walling, Dustin; Ding, Yujie; Xia, Ziyun; Schwendeman, Anna; Hawes, Debra; Yang, Fusheng; Judkins, Alexander R; Wahl, Daniel; Lyssiotis, Costas A; Nava, Daniel de la; Alonso, Marta M; Eze, Augustine; Spitzer, Jasper; Schmidt, Susanne V; Duchatel, Ryan J; Dun, Matthew D; Cain, Jason E; Jiang, Li; Stopka, Sylwia A; Baquer, Gerard; Regan, Michael S; Filbin, Mariella G; Agar, Nathalie Y R; Zhao, Lili; Kumar-Sinha, Chandan; Mody, Rajen; Chinnaiyan, Arul; Kurokawa, Ryo; Pratt, Drew; Yadav, Viveka N; Grill, Jacques; Kline, Cassie; Mueller, Sabine; Resnick, Adam; Nazarian, Javad; Allen, Joshua E; Odia, Yazmin; Gardner, Sharon L; Koschmann, Carl

Chromosomal instability degrades developmental phenotypes essential for anti-GD2 immunotherapy outcomes in high-risk neuroblastoma

染色体不稳定性会降低高危神经母细胞瘤抗GD2免疫疗法疗效所必需的发育表型。

Rebernick, Ryan James; Choi, Jae Eun; Hesse, Calvin; Hosseini, Noshad; Chu, Alec; Zhou, Jin; Ning, Yu; Wang, Rui; Cao, Xuhong; Irwin, Meredith; Wu, Yi-Mi; Kumar, Chandan; Rabah, Raja; Bagatell, Rochelle; Chinnaiyan, Arul M; Mody, Rajen; Cieslik, Marcin

Therapeutic benefit of the dual ALK/FAK inhibitor ESK440 in ALK-driven neuroblastoma.

双重 ALK/FAK 抑制剂 ESK440 在 ALK 驱动的神经母细胞瘤中的治疗益处

Chugh Seema, Tien Jean C, Hon Jennifer, Kenum Carson, Mannan Rahul, Cheng Yunhui, Li Chi Chiang, Taher Zainab I, Delekta Andrew D, Bawa Pushpinder Singh, Apel Ingrid J, Miner Stephanie J, Cao Xuhong, Mehra Rohit, Dhanasekaran Saravana M, Qiao Yuanyuan, Mody Rajen, Chinnaiyan Arul M

Real-world generalizability of clinical trial cytomolecular risk in pediatric acute myeloid leukemia: a report from the REAL-AML cohort

儿童急性髓系白血病临床试验细胞分子风险的真实世界普适性:来自 REAL-AML 队列的报告

Zheng, Daniel J; Hettinger, Gary; Aftandilian, Catherine; Bona, Kira; Caywood, Emi H; Collier, Anderson B; Elgarten, Caitlin W; Gathers, Cody; Ghosh, Taumoha; Gramatges, M Monica; Henry, Meret; Huang, Yuan-Shung V; Li, Yimei; Lotterman, Craig; Maloney, Kelly; Mian, Amir; Miller, Tamara P; Modi, Arunkumar; Mody, Rajen; Morgan, Elaine; Myers, Regina; Newman, Haley; Ortiz, Jose; Seif, Alix E; Smith, Caroline; Stokke, Jamie; Wang, Xin; Winick, Naomi; Wilkes, Jennifer J; Wong, Victor; Aplenc, Richard; Getz, Kelly D

Pediatric Oncology Patients With Germline Pathogenic Variants in Adult-Onset Cancer Predisposition Genes

携带成人发病癌症易感基因种系致病变异的儿科肿瘤患者

Jacobs, Michelle F; Austin, Sarah; Murad, Andrea M; Koeppe, Erika; Kumar-Sinha, Chandan; Robinson, Dan R; Wu, Yi-Mi; Vo, Josh N; Koschmann, Carl; Robertson, Patricia; Franson, Andrea; Leung, Denise; Chinnaiyan, Arul M; Mody, Rajen J

A Phase 1/2 Study of Lenvatinib in Combination With Everolimus in Recurrent and Refractory Pediatric and Young Adult Solid Tumors

乐伐替尼联合依维莫司治疗复发性和难治性儿童及青少年实体瘤的1/2期研究

Dela Cruz, Filemon S; Fox, Elizabeth; DuBois, Steven G; Friedman, Gregory K; Croop, James M; Kim, AeRang; Morgenstern, Daniel A; Balis, Frank M; Macy, Margaret E; Pressey, Joseph G; Watt, Tanya; Krystal, Julie I; Vo, Kieuhoa T; Mody, Rajen; Laetsch, Theodore W; Weigel, Brenda J; O'Hara, Karen; He, Cixin S; Aluri, Jagadeesh; Okpara, Chinyere E; Glade Bender, Julia L

PATH-39. Tail ligation recombinase polymerase amplification sequencing (TLDRseq) enables sensitive, same-day, multi-gene sequencing for plasma-based detection and timely monitoring of brain tumor ctDNA

PATH-39. 尾部连接重组酶聚合酶扩增测序 (TLDRseq) 可实现灵敏、当日完成的多基因测序,用于基于血浆的脑肿瘤循环肿瘤DNA (ctDNA) 检测和及时监测。

Antoniou, Anastasia; Georgiou, Leonidas; Chrysanthou, Antreas; Christofi, Antonis; Roussakis, Yiannis; Ioannides, Cleanthis; Spanoudes, Kyriakos; Zhao, Jufeng; Yu, Liyang; Damianou, Christakis; Liu‐Ambrose, Teresa; Innani, Shubham; Pitarch-Abaigar, Carla; Marwan, Majeed M; Harmsen, Hannah; Bell, W Robert; Makris, Dimitrios; Bakas, Spyridon; Jackson, Devon; Majeed, Marwan; Caldwell, Timothy; Shiue, Kevin; Almeida, Joao Paulo; Gatson, Na Tosha; Harmsen, Hannah; Bell, Robert; Eze, Ucheoma; Wang, Zihan; Ni, Bowen; Wu, Kezhi; Zhang, Qi; Guo, Jinglin; Yang, Runwei; Wang, Ziyu; Yi, Guozhong; Huang, Guanglong; He, Minyi; Xu, Yimin; Liu, Yawei; Brandenburg, Charlotte; Starzetz, Tatjana; Luger, Anna; Singh, Omkar; Aldape, Kenneth D; Schweizer, Leonille; Lachance, Daniel; Paul, Decker; Kollmeyer, Thomas; Drucker, Kristen; Praska, Corinne; Kosel, Matthew; Odukoya, AbdulLateef; Kizilbash, Sani; Maqbool, Asad; Shafqat, Shameel; Tobin, Oliver; Burns, Terry; Parney, Ian; Galanis, Evanthia; Giannini, Caterina; Vaubel, Rachael; Ida, Cris; Jenkins, Robert; Passow, Jeanette Eckel; Shukla, Poojan; Peeran, Zain; Chen, Jia-Shu; Al-Adli, Nadeem; Koshkin, Vadim; Vasudevan, Harish; Morshed, Ramin; Nguyen, Minh; Mirchia, Kanish; Morshed, Ramin; Bush, Nancy Ann Oberheim; Villanueva-Meyer, Javier; Braman, Brooke; Chen, William; Devine, Patrick; Perry, Arie; Raleigh, David; Innani, Shubham; Bell, W Robert; Nasrallah, MacLean P; Baheti, Bhakti; Bakas, Spyridon; Chen, Chao-Hsien; von Bubnoff, Fabian; Leung, Cheuk Hong; Campbell, Erick; Wathoo, Chetna; Lin, Heather; Puduvalli, Vinay K; Majd, Nazanin K; Wadden, Jack; Aittaleb, Rayan; Adam, Tiffany; Jackson, Conner; John, Vishal; Lau, Benison; Calvert, Rebecca; Franson, Andrea; Mody, Rajen; Prensner, John; Upadhyaya, Santhosh; Koschmann, Carl

A road map for the treatment of pediatric diffuse midline glioma

儿童弥漫性中线胶质瘤的治疗路线图

Koschmann, Carl; Al-Holou, Wajd N; Alonso, Marta M; Anastas, Jamie; Bandopadhayay, Pratiti; Barron, Tara; Becher, Oren; Cartaxo, Rodrigo; Castro, Maria G; Chung, Chan; Clausen, Madison; Dang, Derek; Doherty, Robert; Duchatel, Ryan; Dun, Matthew; Filbin, Mariella; Franson, Andrea; Galban, Stefanie; Garcia Moure, Marc; Garton, Hugh; Gowda, Pruthvi; Marques, Joana Graca; Hawkins, Cynthia; Heath, Allison; Hulleman, Esther; Ji, Sunjong; Jones, Chris; Kilburn, Lindsay; Kline, Cassie; Koldobskiy, Michael A; Lim, Daniel; Lowenstein, Pedro R; Lu, Q Richard; Lum, Joanna; Mack, Stephen; Magge, Suresh; Marini, Bernard; Martin, Donna; Marupudi, Neena; Messinger, Dana; Mody, Rajen; Morgan, Meredith; Mota, Mateus; Muraszko, Karin; Mueller, Sabine; Natarajan, Siva Kumar; Nazarian, Javad; Niculcea, Michael; Nuechterlein, Nicholas; Okada, Hideho; Opipari, Valerie; Pai, Manjunath P; Pal, Sharmistha; Peterson, Erik; Phoenix, Timothy; Prensner, John R; Pun, Matthew; Raju, G Praveen; Reitman, Zachary J; Resnick, Adam; Rogawski, David; Saratsis, Amanda; Sbergio, Stefanie G; Souweidane, Mark; Stafford, James M; Tzaridis, Theophilos; Venkataraman, Sujatha; Vittorio, Orazio; Wadden, Jack; Wahl, Daniel; Wechsler-Reya, Robert J; Yadav, Viveka Nand; Zhang, Xu; Zhang, Qiang; Venneti, Sriram

Palbociclib in Solid Tumor Patients With Genomic Alterations in the cyclinD-cdk4/6-INK4a-Rb Pathway: Results From National Cancer Institute-Children's Oncology Group Pediatric Molecular Analysis for Therapy Choice Trial Arm I (APEC1621I)

Palbociclib 治疗具有细胞周期蛋白 D-cdk4/6-INK4a-Rb 通路基因组改变的实体瘤患者:来自美国国家癌症研究所-儿童肿瘤协作组儿科分子分析治疗选择试验组 I (APEC1621I) 的结果

Macy, Margaret E; Mody, Rajen; Reid, Joel M; Piao, Jin; Saguilig, Lauren; Alonzo, Todd A; Berg, Stacey L; Fox, Elizabeth; Weigel, Brenda J; Hawkins, Douglas S; Mooney, Margaret M; Williams, P Mickey; Patton, David R; Coffey, Brent D; Roy-Chowdhuri, Sinchita; Takebe, Naoko; Tricoli, James V; Janeway, Katherine A; Seibel, Nita L; Parsons, D Williams

QLTI-01. ASSESSING THE EFFECTIVENESS OF SUPPORT FROM ST. JUDE CHILDREN’S RESEARCH HOSPITAL TO VIETNAMESE TEAM IN TREATMENT FOR CHILDREN WITH BRAIN TUMORS

QLTI-01. 评估圣裘德儿童研究医院对越南团队在治疗脑瘤患儿方面提供的支持的有效性

Jacobs, Michelle F; Goldman, Joshua W; Austin, Sarah; Koeppe, Erika S; Murad, Andrea M; Koschmann, Carl J; Chinnaiyan, Arul M; Mody, Rajen J; Nguyen, Hoa Thi Kim; Bui, Lan Ngoc; Phan, Duy Canh; Dao, An Thi Thanh; Nguyen, Anh Hoang Mai; Hoang, Thach Ngoc; Do, Thanh Cam; Van Nguyen, Dinh; Handayani, Andini; Blair, Sally; Lam, Catherine G; Qaddoumi, Ibrahim