日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma

ReNeu:一项针对有症状的1型神经纤维瘤病相关丛状神经纤维瘤成人和儿童的米达替尼关键性IIb期试验

Moertel, Christopher L; Hirbe, Angela C; Shuhaiber, Hans H; Bielamowicz, Kevin; Sidhu, Alpa; Viskochil, David; Weber, Michael D; Lokku, Armend; Smith, L Mary; Foreman, Nicholas K; Hajjar, Fouad M; McNall-Knapp, Rene Y; Weintraub, Lauren; Antony, Reuben; Franson, Andrea T; Meade, Julia; Schiff, David; Walbert, Tobias; Ambady, Prakash; Bota, Daniela A; Campen, Cynthia J; Kaur, Gurcharanjeet; Klesse, Laura J; Maraka, Stefania; Moots, Paul L; Nevel, Kathryn; Bornhorst, Miriam; Aguilar-Bonilla, Ana; Chagnon, Sarah; Dalvi, Nagma; Gupta, Punita; Khatib, Ziad; Metrock, Laura K; Nghiemphu, P Leia; Roberts, Ryan D; Robison, Nathan J; Sadighi, Zsila; Stapleton, Stacie; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Reply to: Challenges in Assessing Response in Clinical Trials for Neurofibromatosis Type 1 Plexiform Neurofibromas

回复:评估 1 型神经纤维瘤病丛状神经纤维瘤临床试验疗效的挑战

Moertel, Christopher L; Hirbe, Angela C; Klesse, Laura J; Nghiemphu, P Leia; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Atomoxetine Drug Properties for Repurposing as a Candidate Alzheimer’s Disease Therapeutic Agent

阿托莫西汀的药物特性使其有望成为阿尔茨海默病治疗药物的候选药物

Dammer, Eric B; Read, R; Luis Jimenez Macias, J; Oh, S; Hu, Z; Yin, K; Sele, N; Boon, N; Sing, A; Sloan, S; Yordanov, N Y; Maleki, N; Amiruddin, R; Moawad, A W; Gkampenis, A; Fehringer, P; Umeh, F; Chukwurah, C; Pytlarz, M; Ivory, M; Petrovic, B; Albalooshy, B; Schrickel, E; Memon, F; Cramer, J; Krycia, M; Alotaibi, A; Jakovljevic, M; Guelen, M S; Ghonim, M; Ghonim, M; Page, N; Mhana, S; Baid, U; Lohmann, P; Bakas, S; Aboian, M; Babovic-Vuksanovic, D; Moertel, C L; Shuhaiber, H H; Viskochil, D; Sidhu, A; Meade, J; Hirbe, A C; Weintraub, L; Langseth, A J; Weber, M D; Lokku, A; Hajjar, F M; Antony, R; Schiff, D; Raslan, A M; Nevel, K; Gershon, T R; Demsey, Laura L; Burch, Danielle; Lin, Evan; Quach, Diana; Podvin, Sonia; Boyarko, Ben; Levey, Allan I; Weinshenker, David; Edland, Steven; Galasko, Douglas; Jacobs, Heidi; Bang, Anne; Neil, Ashley; Silverman, James; Feldman, Howard H; Hook, Vivian

Clinical Characteristics and Outcomes of Central Nervous System Tumors Harboring NTRK Gene Fusions

携带NTRK基因融合的中枢神经系统肿瘤的临床特征和预后

Lamoureux, Audrey-Anne; Fisher, Michael J; Lemelle, Lauriane; Pfaff, Elke; Amir-Yazdani, Pouneh; Kramm, Christof; De Wilde, Bram; Kazanowska, Bernarda; Hutter, Caroline; Pfister, Stefan M; Sturm, Dominik; Jones, David T W; Orbach, Daniel; Pierron, Gaëlle; Raskin, Scott; Drilon, Alexander; Diamond, Eli L; Harada, Guilherme; Zapotocky, Michal; Zamecnik, Josef; Krskova, Lenka; Ellezam, Benjamin; Weil, Alexander G; Venne, Dominic; Barritault, Marc; Leblond, Pierre; Coltin, Hallie; Hammad, Rawan; Tabori, Uri; Hawkins, Cynthia; Hansford, Jordan R; Meyran, Deborah; Erker, Craig; McFadden, Kathryn; Sato, Mariko; Gottardo, Nicholas G; Dholaria, Hetal; Nørøxe, Dorte Schou; Goto, Hiroaki; Ziegler, David S; Lin, Frank Y; Parsons, Donald Williams; Lindsay, Holly; Wong, Tai-Tong; Liu, Yen-Lin; Wu, Kuo-Sheng; Franson, Andrea T; Hwang, Eugene; Aguilar-Bonilla, Ana; Cheng, Sylvia; Cacciotti, Chantel; Massimino, Maura; Schiavello, Elisabetta; Wood, Paul; Hoffman, Lindsey M; Cappellano, Andréa; Lassaletta, Alvaro; Van Damme, An; Llort, Anna; Gerber, Nicolas U; Spalato Ceruso, Mariella; Bendel, Anne E; Skrypek, Maggie; Hamideh, Dima; Mushtaq, Naureen; Walter, Andrew; Jabado, Nada; Alsahlawi, Aysha; Farmer, Jean-Pierre; Coleman, Christina; Mueller, Sabine; Mazewski, Claire; Aguilera, Dolly; Robison, Nathan J; O'Halloran, Katrina; Abbou, Samuel; Berlanga, Pablo; Geoerger, Birgit; Øra, Ingrid; Moertel, Christopher L; Razis, Evangelia D; Vernadou, Anastasia; Ducray, François; Bronnimann, Charlotte; Seizeur, Romuald; Clarke, Matthew; Resnick, Adam C; Alves, Mélanie; Jones, Chris; Doz, François; Laetsch, Theodore W; Perreault, Sébastien

NFS-24. TUMOR VOLUME IN NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1 (NF1-OPG): PRELIMINARY RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY

NFS-24. 与NF1相关的视路胶质瘤(NF1-OPG)新诊断肿瘤体积:国际多中心NF1-OPG自然史研究的初步结果

O'Neill, Matthew J; Ng, Chai-Ann; Aizawa, Takanori; Sala, Luca; Bains, Sahej; Winbo, Annika; Ullah, Rizwan; Shen, Qianyi; Tan, Chek-Ying; Kozek, Krystian; Vanags, Loren R; Mitchell, Devyn W; Shen, Alex; Wada, Yuko; Kashiwa, Asami; Crotti, Lia; Dagradi, Federica; Musu, Giulia; Spazzolini, Carla; Neves, Raquel; Bos, J Martijn; Giudicessi, John R; Bledsoe, Xavier; Gamazon, Eric R; Lancaster, Megan; Glazer, Andrew M; Knollmann, Bjorn C; Roden, Dan M; Weile, Jochen; Roth, Frederick; Salem, Joe-Elie; Earle, Nikki; Stiles, Rachael; Agee, Taylor; Johnson, Christopher N; Horie, Minoru; Skinner, Jonathan; Ackerman, Michael J; Schwartz, Peter J; Ohno, Seiko; Vandenberg, Jamie I; Kroncke, Brett M; Fisher, Michael J; de Blank, Peter; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borcher, March; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; El-Dairi, Mays; Van Mater, David; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Oattes, Julius; Reddy, Alyssa; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Cutter, Gary; Avery, Robert; Levine, Adrian; Bennett, Julie; Li, Cyril; Rana, Mansuba; Yuditskiy, Richard; Ho, I-Chen; Haizel-Cobbina, Joseline; Hansford, Jordan; Luck, Amanda; Ludlow, Louise; Eisenstat, David; Toledano, Helen; Masoud, Roaya; Fukuoka, Kohei; Yamasaki, Kai; Nakano, Yoshiko; Mushtaq, Naureen; Minhas, Khurram; Bukhari, Syed Ibrahim; Stuecklin, Ana Guerreiro; Weiser, Annette; Jadrijevic-Cvilje, Filip; Fleming, Adam; Campbell, Shawde; Cacciotti, Chantel; Erker, Craig; van Landeghem, Frank; Wilson, Bev; Black, Karina; MacNeil, Mary; Cheng, Sylvia; Dunham, Chris; Larouche, Valerie; Giannakouros, Panagiota; Fonseca, Adriana; Williamson, Lane; Plant-Fox, Ashley; Levy, Jean Mulcahy; DeMarsh, Samantha; Vega, José Velázquez; Patil, Prabhumallikarjun; Nasrallah, MacLean; Santi-Vicini, Mariarita; Nelson, Ernest; Graham, Richard; Raskin, Scott; Fernandes, Igor; Dewan, Michael; Tabori, Uri; Hawkins, Cynthia; Senapati, Akanksha; Lindsay, Holly; Gilheeney, Stephen; Bale, Tejus; Taylor, Michael; Khuong-Quang, Dong-Anh; Bouffet, Eric; Khan, Sara; van Veelan, Marie-Lise; Kros, Johan M; Vasiljevic, Alexandre; Pollack, Ian; Chambless, Lola; Gupta, Nalin; Weiss, William A; Jabado, Nada; Sterba, Jaroslav; Zapotocky, Michal; Hansford, Jordan R; Ramaswamy, Vijay; Mikkelsen, Margit; Li, Xiaoyu; Yu, Kaiwen; High, Anthony; Tran, Haiyan; Furtado, Larissa V; Leelatian, Nalin; Berry, Julia D; Mobley, Bret C; Dewan, Michael C; May, Adriana; Kofler, Julia; Foster, Jessica; Lazow, Margot; Boué, Daniel R; Qaddoumi, Ibrahim; Robinson, Giles W; Peng, Junmin; Moreira, Daniel C; Chiang, Jason; Avery, Robert; Jiang, Zhifan; Parida, Abhijeet; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; de Blank, Peter; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borchert, Mark; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; Van Mater, David; El-Diari, Mays; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Oattes, Julius; Reddy, Alyssa; Cutter, Gary; Linguraru, Marius; Fisher, Michael

NFS-24. TUMOR VOLUME IN NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1 (NF1-OPG): PRELIMINARY RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY

NFS-24. 与NF1相关的视路胶质瘤(NF1-OPG)新诊断肿瘤体积:国际多中心NF1-OPG自然史研究的初步结果

Ladbury, Colton; Semwal, Hemal; Hong, Daniel; Yang, Dongyun; Hao, Claire; Han, Chunhui; Liu, An; Marcucci, Guido; Rosenthal, Joseph; Hui, Susanta; Salhotra, Amandeep; Ali, Haris; Nakamura, Ryotaro; Stein, Anthony; Al Malki, Monzr; Wong, Jeffrey Y C; Dandapani, Savita; Ahluwalia, Manmeet; Ozair, Ahmad; Bardhan, Mainak; Bellur, Shreyas; Starosciak, Amy; Perche, Dilanis; Khosla, Atulya; Leon-Ariza, Daniel; Rubens, Muni; Odia, Yazmin; Mehta, Minesh; Kotecha, Rupesh; McDermott, Michael; Sandoval-Leon, Ana; Mahtani, Reshma; Peereboom, David; Busquets, F Bossacoma; Genestar, JL Vinent; Llobet, A Ruiz; Passini, VP Celis; Pasqual, N Arranz; Comes, A; Suárez, J Arrojo; Celma, M Sácnhez; Moss, Nelson S; Imber, Brandon S; Prasad, Kavya; Chu, Bae P; Goel, Arun; Aramburu-Nunez, David; Bellamy, Michael; Yang, T Jonathan; Khan, Atif J; Dauer, Laurence T; Cohen, Gilad N; Beal, Kathryn; Tabar, Viviane; Avery, Robert; Jiang, Zhifan; Parida, Abhijeet; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; de Blank, Peter; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borchert, Mark; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; Van Mater, David; El-Diari, Mays; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Oattes, Julius; Reddy, Alyssa; Cutter, Gary; Linguraru, Marius; Fisher, Michael

NFS-21. DEMOGRAPHIC, CLINICAL AND IMAGING CHARACTERISTICS OF NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1: RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY

NFS-21. 与 NF1 相关的新诊断视路胶质瘤的人口统计学、临床和影像学特征:来自国际多中心 NF1-OPG 自然史研究的结果

Thompson, R Houston; Eastham, James A; Scardino, Peter T; Sheinfeld, Joel; Fisher, Michael J; de Blank, Peter; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borcher, March; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; El-Dairi, Mays; Van Mater, David; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Oattes, Julius; Reddy, Alyssa; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Cutter, Gary; Avery, Robert

The 8th International RASopathies Symposium: Expanding research and care practice through global collaboration and advocacy

第八届国际RAS病研讨会:通过全球合作与倡导拓展研究和治疗实践

Pierpont, Elizabeth I; Bennett, Anton M; Schoyer, Lisa; Stronach, Beth; Anschutz, April; Borrie, Sarah C; Briggs, Benjamin; Burkitt-Wright, Emma; Castel, Pau; Cirstea, Ion C; Draaisma, Fieke; Ellis, Michelle; Fear, Vanessa S; Frone, Megan N; Flex, Elisabetta; Gelb, Bruce D; Green, Tamar; Gripp, Karen W; Khoshkhoo, Sattar; Kieran, Mark W; Kleemann, Karolin; Klein-Tasman, Bonita P; Kontaridis, Maria I; Kruszka, Paul; Leoni, Chiara; Liu, Clifford Z; Merchant, Nadia; Magoulas, Pilar L; Moertel, Christopher; Prada, Carlos E; Rauen, Katherine A; Roelofs, Renée; Rossignol, Rodrigue; Sevilla, Christine; Sevilla, Gigi; Sheedy, Ryan; Stieglitz, Elliot; Sun, Daochun; Tiemens, Dagmar; White, Forest; Wingbermühle, Ellen; Wolf, Cordula; Zenker, Martin; Andelfinger, Gregor

The OTX2 Gene Induces Tumor Growth and Triggers Leptomeningeal Metastasis by Regulating the mTORC2 Signaling Pathway in Group 3 Medulloblastomas

OTX2基因通过调节3组髓母细胞瘤中的mTORC2信号通路诱导肿瘤生长并触发软脑膜转移

Elisabet Ampudia-Mesias ,Charles S Cameron ,Eunjae Yoo ,Marcus Kelly ,Sarah M Anderson ,Riley Manning ,Juan E Abrahante Lloréns ,Christopher L Moertel ,Hyungshin Yim ,David J Odde ,Nurten Saydam ,Okay Saydam

CTNI-21. PIVOTAL, PHASE 2B RENEU TRIAL OF MIRDAMETINIB IN CHILDREN AND ADULTS WITH NEUROFIBROMATOSIS TYPE 1-ASSOCIATED PLEXIFORM NEUROFIBROMA (NF1-PN): A SPOTLIGHT ON PATIENTS ACHIEVING DEEP RESPONSE

CTNI-21. 针对患有 1 型神经纤维瘤病相关丛状神经纤维瘤 (NF1-PN) 的儿童和成人的 MIRDAMETINIB 关键性 2b 期 RENEU 试验:聚焦获得深度缓解的患者

Gorrepati, Venkata Subhash; Yang, Dennis; Draganov, Peter V; Marcella, Stephen; Kobic, Emir; Carr, Amy L; Georgiades, Benjamin; Margiotta, Caroline; Ackley, Renee; Roshdy, Danya; Isip, Jacqueline; Minor, Sarah B,; Elchynski, Amanda L; Anderson, William E; Capraro, Gerald A; Polk, Christopher; Marx, Ashley H; Chundi, Vahini; Zaccardelli, Jill; Angle, Timothy; Oriet, Jonathan; Swartwood, Michael J; Boyce, Ross; Daniels, Lindsay M; Juliano, Jonathan J; Gershon, Timothy; Moertel, Christopher; McNall-Knapp, Rene; Shuhaiber, Hans; Weintraub, Lauren; Hajjar, Fouad; Nickerson, Molly; Weber, Michael; Lokku, Armend; Babovic-Vuksanovic, Dusica; Hirbe, Angela