日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Implications of the FDA's new plausible mechanism framework for the development of a personalized in vivo prime editing platform

FDA新的合理机制框架对开发个性化体内先导基因编辑平台的影响

Feierman, Emily R; Whittaker, Madelynn N; Quigley, Aidan; Brooks, Dominique L; McVeigh, Paige; Nan, Angela X; Hsu, Alvin; Said, Hooda; Soliman, Ousamah Younoss; Giovenco, Ryan; Davidson, Beverly L; Alameh, Mohamad-Gabriel; Liu, David R; Wang, Xiao; Musunuru, Kiran; Ahrens-Nicklas, Rebecca C

Investigating the impact of hypoxia and syncytialization on lipid nanoparticle-mediated mRNA delivery to placental cells

研究缺氧和合胞体化对脂质纳米颗粒介导的mRNA向胎盘细胞递送的影响

Young, Rachel E; Vijayakumar, Tara; Reilley, Logan J; Darji, Krisha; Patel, Diya; Hofbauer, Samuel; Alameh, Mohamad-Gabriel; Weissman, Drew; Riley, Rachel

Correction of a recurrent pathogenic variant in methylmalonic acidemia using adenine base editing

利用腺嘌呤碱基编辑技术纠正甲基丙二酸血症中的复发性致病变异

Kahn, Elena M; Said, Hooda; Qu, Ping; Alameh, Mohamad-Gabriel; Wang, Xiao; Musunuru, Kiran; Ahrens-Nicklas, Rebecca C

Evaluation of an H5 influenza virus mRNA-lipid nanoparticle (LNP) vaccine in lactating dairy cows

在泌乳奶牛中评估H5流感病毒mRNA-脂质纳米颗粒(LNP)疫苗

Santos, Jefferson J S; Souza, Carine K; Zanella, Giovana C; Goulart, Débora B; Arruda, Bailey; Boggiatto, Paola; Palmer, Mitchell V; Snyder, Celeste A; Kristula, Michaela A; Dickens, Charlene; Webb, Terry L; Atkinson, Reilly K; Dadonaite, Bernadeta; Dwivedi, Garima; Alameh, Mohamad-Gabriel; Bloom, Jesse D; Weissman, Drew; Althouse, Gary C; Baker, Amy L; Hensley, Scott E

Generation and characterization of a novel MHC-II tetramer for tracking and characterization of toxin B-specific CD4(+) T cell responses

生成并表征一种新型MHC-II四聚体,用于追踪和表征毒素B特异性CD4(+) T细胞反应

Maslanka, Jeffrey R; She, Qianxuan; Krauss, Kathleen S; Konopka, Emily N; Bayard, Nile U; Londregan, Jennifer; Alameh, Mohamad-Gabriel; Eisenlohr, Laurence C; Kutzler, Michele A; Zackular, Joseph P; Abt, Michael C

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease

利用患者特异性体内基因编辑技术治疗罕见遗传疾病

Musunuru, Kiran; Grandinette, Sarah A; Wang, Xiao; Hudson, Taylor R; Briseno, Kevin; Berry, Anne Marie; Hacker, Julia L; Hsu, Alvin; Silverstein, Rachel A; Hille, Logan T; Ogul, Aysel N; Robinson-Garvin, Nancy A; Small, Juliana C; McCague, Sarah; Burke, Samantha M; Wright, Christina M; Bick, Sarah; Indurthi, Venkata; Sharma, Shweta; Jepperson, Michael; Vakulskas, Christopher A; Collingwood, Michael; Keogh, Katie; Jacobi, Ashley; Sturgeon, Morgan; Brommel, Christian; Schmaljohn, Ellen; Kurgan, Gavin; Osborne, Thomas; Zhang, He; Kinney, Kyle; Rettig, Garrett; Barbosa, Christopher J; Semple, Sean C; Tam, Ying K; Lutz, Cathleen; George, Lindsey A; Kleinstiver, Benjamin P; Liu, David R; Ng, Kim; Kassim, Sadik H; Giannikopoulos, Petros; Alameh, Mohamad-Gabriel; Urnov, Fyodor D; Ahrens-Nicklas, Rebecca C

Placenta-tropic VEGF mRNA lipid nanoparticles ameliorate murine pre-eclampsia.

胎盘趋向性 VEGF mRNA 脂质纳米颗粒可改善小鼠先兆子痫

Swingle Kelsey L, Hamilton Alex G, Safford Hannah C, Geisler Hannah C, Thatte Ajay S, Palanki Rohan, Murray Amanda M, Han Emily L, Mukalel Alvin J, Han Xuexiang, Joseph Ryann A, Ghalsasi Aditi A, Alameh Mohamad-Gabriel, Weissman Drew, Mitchell Michael J

Combinatorial design of siloxane-incorporated lipid nanoparticles augments intracellular processing for tissue-specific mRNA therapeutic delivery

通过组合设计将硅氧烷掺入脂质纳米颗粒,可增强细胞内加工,从而实现组织特异性mRNA治疗递送。

Lulu Xue # ,Gan Zhao # ,Ningqiang Gong # ,Xuexiang Han ,Sarah J Shepherd ,Xinhong Xiong ,Zebin Xiao ,Rohan Palanki ,Junchao Xu ,Kelsey L Swingle ,Claude C Warzecha ,Rakan El-Mayta ,Vivek Chowdhary ,Il-Chul Yoon ,Jingcheng Xu ,Jiaxi Cui ,Yi Shi ,Mohamad-Gabriel Alameh ,Karin Wang ,Lili Wang ,Darrin J Pochan ,Drew Weissman ,Andrew E Vaughan ,James M Wilson ,Michael J Mitchell

An Il12 mRNA-LNP adjuvant enhances mRNA vaccine-induced CD8 T cell responses

IL-12 mRNA-LNP佐剂可增强mRNA疫苗诱导的CD8 T细胞反应

Aunins, Emily A; Phan, Anthony T; Alameh, Mohamad-Gabriel; Dwivedi, Garima; Cruz-Morales, Elisa; Christian, David A; Tam, Ying; Bunkofske, Molly E; Peñafiel, Anabel Zabala; O'Dea, Keenan M; Merolle, Maria; Furey, Colleen; Scott, Phillip; Vonderheide, Robert H; Hensley, Scott E; Kedl, Ross M; Weissman, Drew; Hunter, Christopher A

Multiarm-Assisted Design of Dendron-like Degradable Ionizable Lipids Facilitates Systemic mRNA Delivery to the Spleen

利用多臂辅助设计树枝状可降解电离脂质体,促进mRNA向脾脏的系统性递送

Xue, Lulu; Xiong, Xinhong; Zhao, Gan; Molina-Arocho, William; Palanki, Rohan; Xiao, Zebin; Han, Xuexiang; Yoon, Il-Chul; Figueroa-Espada, Christian G; Xu, Junchao; Gong, Ningqiang; Shi, Qiangqiang; Chen, Qinyuan; Alameh, Mohamad-Gabriel; Vaughan, Andrew E; Haldar, Malay; Wang, Karin; Weissman, Drew; Mitchell, Michael J