Bioengineered AAV9 and Optimised Microdystrophin Vectors Augment Phenotypic Rescue in a Murine Model of Duchenne Muscular Dystrophy
生物工程改造的AAV9和优化的微型肌营养不良蛋白载体增强了杜氏肌营养不良小鼠模型的表型恢复
期刊:Journal of Cellular and Molecular Medicine
影响因子:4.2
doi:10.1111/jcmm.71078
Senthilkumar, Mohankumar B; Sharma, Sanya; Srinivasan, Navaneeth; Varghese, Anila; Sarangi, Pratiksha; Singh, Vijayata; Kumar, Narendra; Yenurkar, Devyani; Mukherjee, Sudip; Amit, Sonal; Bhatia, Sameer; Misra, Santosh K; Puri, Ratna Dua; Chamberlain, Jeffrey; Jayandharan, Giridhara R