Modeling Adeno-Associated Viral Vector 6-mediated In Vivo Gene Delivery to Expanded Non-Mobilized Haemopoietic Stem Cells from Transfusion-dependent Thalassemia Patients in a Humanized Mouse
在人源化小鼠中模拟腺相关病毒载体6介导的体内基因递送至输血依赖型地中海贫血患者扩增的非动员造血干细胞
期刊:
影响因子:
doi:10.1101/2025.06.17.659025
Ramesh, Janani; Kandasamy, Karthikeyan; Yusof, Nur Nazneen; Sujuandy, Ihsan; Keng, Choong Tat; Chen, Liwei; Chia, Bing Shao; Liu, Min; Her, Zhisheng; Kukumberg, Marek; Sia, Kian Chuan; Mohd Rodhi, Siti Humairah; Fu, Zhen Ying; Rufaihah, A J; Franco-Obregón, Alfredo; Choolani, Mahesh; Sesurajan, Binny Priya; Lai, Poh-San; Lee, Shir Ying; Koh, Pei Lin; Chen, Qingfeng; Gan, Shu-Uin; Chew, Wei Leong; Mattar, Citra Nz
微生物学
代谢
Human
细胞生物学
Mouse
发育与干细胞
干细胞
贫血
