Longitudinal multi-omics profiling of spinal muscular atrophy
脊髓性肌萎缩症的纵向多组学分析
期刊:Neurotherapeutics
影响因子:6.9
doi:10.1016/j.neurot.2026.e00880
Dabaj, Ivana; Nguyen, Thi Hai Yen; Lagrue, Emmanuelle; Ducatez, Franklin; Allouche, Stéphane; Ausseil, Jérôme; Seferian, Andreea; Gomez-Garcia de la Banda, Marta; Benezit, Audrey; Phelep, Aurélie; Chouchane, Mondher; Vasseur, Stéphane; Chapart, Maud; Marret, Stéphane; Quijano Roy, Susana; Tebani, Abdellah; Bekri, Soumeya