Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
Inotersen治疗遗传性转甲状腺素蛋白淀粉样变性患者
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa1716793
Benson, Merrill D; Waddington-Cruz, Márcia; Berk, John L; Polydefkis, Michael; Dyck, Peter J; Wang, Annabel K; Planté-Bordeneuve, Violaine; Barroso, Fabio A; Merlini, Giampaolo; Obici, Laura; Scheinberg, Morton; Brannagan, Thomas H 3rd; Litchy, William J; Whelan, Carol; Drachman, Brian M; Adams, David; Heitner, Stephen B; Conceição, Isabel; Schmidt, Hartmut H; Vita, Giuseppe; Campistol, Josep M; Gamez, Josep; Gorevic, Peter D; Gane, Edward; Shah, Amil M; Solomon, Scott D; Monia, Brett P; Hughes, Steven G; Kwoh, T Jesse; McEvoy, Bradley W; Jung, Shiangtung W; Baker, Brenda F; Ackermann, Elizabeth J; Gertz, Morie A; Coelho, Teresa