日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: AAV-based delivery of RNAi targeting ataxin-2 improves survival and pathology in TDP-43 mice

作者更正:基于腺相关病毒(AAV)的RNAi靶向ataxin-2可改善TDP-43小鼠的存活率和病理状况。

Amado, Defne A; Robbins, Ashley B; Whiteman, Katherine R; Smith, Alicia R; Chillon, Guillem; Chen, Yonghong; Fuller, Joshua A; Patty, Nicholas A; Izda, Aleksandar; Cheng, Congsheng; Nelson, Shareen; Dichter, Abigail I; Mazzoni, Esteban O; Monteys, Alex Mas; Davidson, Beverly L

AAV-based delivery of RNAi targeting ataxin-2 improves survival and pathology in TDP-43 mice.

基于 AAV 的 RNAi 递送靶向 ataxin-2 可改善 TDP-43 小鼠的生存率和病理状况

Amado Defne A, Robbins Ashley B, Whiteman Katherine R, Smith Alicia R, Chillon Guillem, Chen Yonghong, Fuller Joshua A, Patty Nicholas A, Izda Aleksandar, Cheng Congsheng, Nelson Shareen, Dichter Abigail I, Mazzoni Esteban O, Monteys Alex Mas, Davidson Beverly L

Haplotyping SNPs for allele-specific gene editing of the expanded huntingtin allele using long-read sequencing

利用长读长测序技术对扩增的亨廷顿等位基因进行单倍型SNP分析,以实现等位基因特异性基因编辑。

Fang, Li; Monteys, Alex Mas; Dürr, Alexandra; Keiser, Megan; Cheng, Congsheng; Harapanahalli, Akhil; Gonzalez-Alegre, Pedro; Davidson, Beverly L; Wang, Kai

Erratum: Haplotyping SNPs for allele-specific gene editing of the expanded huntingtin allele using long-read sequencing

勘误:利用长读长测序技术对扩增的亨廷顿等位基因进行等位基因特异性基因编辑的单倍型SNP进行分析

Fang, Li; Monteys, Alex Mas; Dürr, Alexandra; Keiser, Megan; Cheng, Congsheng; Harapanahalli, Akhil; Gonzalez-Alegre, Pedro; Davidson, Beverly L; Wang, Kai

Limited astrocyte-to-neuron conversion in the mouse brain using NeuroD1 overexpression

利用NeuroD1过表达限制小鼠脑内星形胶质细胞向神经元的转化

Leib, David; Chen, Yong Hong; Monteys, Alex Mas; Davidson, Beverly L

DeepRepeat: direct quantification of short tandem repeats on signal data from nanopore sequencing

DeepRepeat:直接定量纳米孔测序信号数据中的短串联重复序列

Fang, Li; Liu, Qian; Monteys, Alex Mas; Gonzalez-Alegre, Pedro; Davidson, Beverly L; Wang, Kai

Single nucleotide seed modification restores in vivo tolerability of a toxic artificial miRNA sequence in the mouse brain

单核苷酸种子修饰可恢复小鼠脑内对有毒人工miRNA序列的体内耐受性

Monteys, Alex Mas; Spengler, Ryan M; Dufour, Brett D; Wilson, Matt S; Oakley, Clayton K; Sowada, Matt J; McBride, Jodi L; Davidson, Beverly L