日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe Phenotype

理论上可通过外显子53跳跃治疗的非行走型杜氏肌营养不良症患者表现出严重的表型

期刊:Journal of Neuromuscular Diseases
影响因子:3.4
doi:10.3233/JND-150100
Servais, Laurent; Montus, Marie; Guiner, Caroline Le; Ben Yaou, Rabah; Annoussamy, Mélanie; Moraux, Amélie; Hogrel, Jean-Yves; Seferian, Andreea M; Zehrouni, Karima; Le Moing, Anne-Gaëlle; Gidaro, Teresa; Vanhulle, Catherine; Laugel, Vincent; Butoianu, Nina; Cuisset, Jean-Marie; Sabouraud, Pascal; Cances, Claude; Klein, Andrea; Leturcq, France; Moullier, Philippe; Voit, Thomas
发表日期：2015
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A 10 patient case report on the impact of plasmapheresis upon neutralizing factors against adeno-associated virus (AAV) types 1, 2, 6, and 8

一份关于血浆置换对腺相关病毒（AAV）1、2、6和8型中和因子影响的10例患者病例报告

期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2011.108
Monteilhet, Virginie; Saheb, Samir; Boutin, Sylvie; Leborgne, Christian; Veron, Philippe; Montus, Marie-Françoise; Moullier, Philippe; Benveniste, Olivier; Masurier, Carole
微生物学
发表日期：2011
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Evidence for long-term efficacy and safety of gene therapy for Wiskott-Aldrich syndrome in preclinical models.

基因疗法治疗威斯科特-奥尔德里奇综合征的临床前模型长期疗效和安全性证据

期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2009.31
Marangoni Francesco, Bosticardo Marita, Charrier Sabine, Draghici Elena, Locci Michela, Scaramuzza Samantha, Panaroni Cristina, Ponzoni Maurilio, Sanvito Francesca, Doglioni Claudio, Liabeuf Marie, Gjata Bernard, Montus Marie, Siminovitch Katherine, Aiuti Alessandro, Naldini Luigi, Dupré Loïc, Roncarolo Maria Grazia, Galy Anne, Villa Anna
发表日期：2009
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