日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Characterization of factors that influence rAAV yield and quality when produced using rHSV co-infection.

利用 rHSV 共感染生产 rAAV 时影响其产量和质量的因素的特征分析

E Xiaofei, Wright Benjamin, Collins Brian E, Peters Lauren, Rose Sviatlana, Webster Peter, Morris Carl A, McGonigle Sharon

N-terminal titin fragment: a non-invasive, pharmacodynamic biomarker for microdystrophin efficacy

N端肌联蛋白片段:一种用于评估微型肌营养不良蛋白疗效的非侵入性药效学生物标志物

Boehler, Jessica F; Brown, Kristy J; Ricotti, Valeria; Morris, Carl A

Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy

在杜氏肌营养不良症GRMD模型中评估全身性AAV-微型肌营养不良蛋白基因治疗

Birch, Sharla M; Lawlor, Michael W; Conlon, Thomas J; Guo, Lee-Jae; Crudele, Julie M; Hawkins, Eleanor C; Nghiem, Peter P; Ahn, Mihye; Meng, Hui; Beatka, Margaret J; Fickau, Brittany A; Prieto, Juan C; Styner, Martin A; Struharik, Michael J; Shanks, Courtney; Brown, Kristy J; Golebiowski, Diane; Bettis, Amanda K; Balog-Alvarez, Cynthia J; Clement, Nathalie; Coleman, Kirsten E; Corti, Manuela; Pan, Xiufang; Hauschka, Stephen D; Gonzalez, J Patrick; Morris, Carl A; Schneider, Joel S; Duan, Dongsheng; Chamberlain, Jeffrey S; Byrne, Barry J; Kornegay, Joe N

Erratum: Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice

更正:自愿轮跑可辅助微型肌营养不良蛋白基因疗法改善 mdx 小鼠的肌肉功能

Hamm, Shelby E; Fathalikhani, Daniel D; Bukovec, Katherine E; Addington, Adele K; Zhang, Haiyan; Perry, Justin B; McMillan, Ryan P; Lawlor, Michael W; Prom, Mariah J; Vanden Avond, Mark A; Kumar, Suresh N; Coleman, Kirsten E; Dupont, J B; Mack, David L; Brown, David A; Morris, Carl A; Gonzalez, J Patrick; Grange, Robert W

Dystrophic muscle improvement in zebrafish via increased heme oxygenase signaling

通过增强血红素加氧酶信号传导改善斑马鱼的营养不良性肌肉

Kawahara, Genri; Gasperini, Molly J; Myers, Jennifer A; Widrick, Jeffrey J; Eran, Alal; Serafini, Peter R; Alexander, Matthew S; Pletcher, Mathew T; Morris, Carl A; Kunkel, Louis M

Thin filament activation and unloaded shortening velocity of rabbit skinned muscle fibres

兔去皮肌纤维细丝激活和无负荷缩短速度

Morris, Carl A; Tobacman, Larry S; Homsher, Earl