日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Chimeric CD3ζ chains containing CD28 signalling motifs enhance antigen-specific IL-2 production and expansion of human TCR-engineered T cells in vitro

含有CD28信号基序的嵌合CD3ζ链可增强抗原特异性IL-2的产生,并促进人TCR工程化T细胞在体外的扩增。

Burgess, Samuel J; Stauss, Hans J; Morris, Emma C

Dominant negative variants in ITPR3 impair T cell Ca2+ dynamics causing combined immunodeficiency.

ITPR3 中的显性负性变异会损害 T 细胞 Ca2+ 动力学,导致联合免疫缺陷

Blanco Elena, Camps Carme, Bahal Sameer, Kerai Mohit D, Ferla Matteo P, Rochussen Adam M, Handel Adam E, Golwala Zainab M, Spiridou Goncalves Helena, Kricke Susanne, Klein Fabian, Zhang Fang, Zinghirino Federica, Evans Grace, Keane Thomas M, Lizot Sabrina, Kusters Maaike A A, Iro Mildred A, Patel Sanjay V, Morris Emma C, Burns Siobhan O, Radcliffe Ruth, Vasudevan Pradeep, Price Arthur, Gillham Olivia, Valdebenito Gabriel E, Stewart Grant S, Worth Austen, Adams Stuart P, Duchen Michael, André Isabelle, Adams David J, Santili Giorgia, Gilmour Kimberly C, Holländer Georg A, Davies E Graham, Taylor Jenny C, Griffiths Gillian M, Thrasher Adrian J, Dhalla Fatima, Kreins Alexandra Y

Allogeneic hematopoietic stem cell transplantation for STAT3 hyper-IgE syndrome: a worldwide study

异基因造血干细胞移植治疗STAT3高IgE综合征:一项全球性研究

Tsilifis, Christo; Raedler, Johannes; Renke, Joanna; Medinger, Michael; Laberko, Alexandra; Haraldsson, Ásgeir; Patel, Niraj; Ciznar, Peter; Wong, Melanie; Keogh, Steven J; Gray, Paul; Mitchell, Richard; Bigley, Venetia; Elcombe, Suzanne; Hauck, Fabian; Albert, Michael H; Tholouli, Eleni; Herwadkar, Archana; Elkhalifa, Shuayb; Kosmidis, Chris; Callisti, Giorgio; Burroughs, Lauri M; Chen, Karin; Carpenter, Ben; Fox, Thomas A; Morris, Emma C; Uppuluri, Ramya; Raj, Revathi; Yanagimachi, Masakatsu; Buddingh, Emilie P; Oikonomopoulou, Christina; Gonzalez, Corina; Dimitrova, Dimana; Kanakry, Jennifer A; Arnold, Danielle; Pai, Sung-Yun; Slatter, Mary A; Pearce, Mark S; Worth, Austen; Freeman, Alexandra F; Gennery, Andrew R

The T385M STAT1 gain-of-function mutation confers the most severe disease outcomes

T385M STAT1 功能获得性突变会导致最严重的疾病后果。

Torrance, Robert; McKenna, Alexander J; King, Catherine; McDowell, Joe; O'Callaghan, Eleanor; Maimaris, Jesmeen; Albuquerque, Adriana S; Pearce, Rachel; Morris, Emma C; Burns, Siobhan O

Pre-Transplant Immune Dysregulation Predicts for Poor Outcome Following Allogeneic Haematopoietic Stem Cell Transplantation in Adolescents and Adults with Inborn Errors of Immunity (IEI)

移植前免疫失调预示着患有先天性免疫缺陷(IEI)的青少年和成人接受异基因造血干细胞移植后预后不良

Fox, Thomas A; Massey, Valerie; Lever, Charley; Pearce, Rachel; Laurence, Arian; Grace, Sarah; Oliviero, Filippo; Workman, Sarita; Symes, Andrew; Lowe, David M; Fiaccadori, Valeria; Hough, Rachael; Tadros, Susan; Burns, Siobhan O; Seidel, Markus G; Carpenter, Ben; Morris, Emma C

Correction to: Pre-Transplant Immune Dysregulation Predicts for Poor Outcome Following Allogeneic Haematopoietic Stem Cell Transplantation in Adolescents and Adults with Inborn Errors of Immunity (IEI)

更正:移植前免疫失调预示着患有先天性免疫缺陷(IEI)的青少年和成人接受异基因造血干细胞移植后预后不良

Fox, Thomas A; Massey, Valerie; Lever, Charley; Pearce, Rachel; Laurence, Arian; Grace, Sarah; Oliviero, Filippo; Workman, Sarita; Symes, Andrew; Lowe, David M; Fiaccadori, Valeria; Hough, Rachael; Tadros, Susan; Burns, Siobhan O; Seidel, Markus G; Carpenter, Ben; Morris, Emma C

Patient-reported outcomes in patients with hematologic malignancies treated with CAR T-cell therapy in Europe

欧洲接受 CAR-T 细胞疗法治疗的血液系统恶性肿瘤患者的患者报告结局

Pennings, Elise R A; Spanjaart, Anne M; Thielen, Frederick W; Oerlemans, Simone; Fleischer, Anna; Sanges, Carmen; Gomes Da Silva, Maria; Cabrerizo, Yolanda; Lecot, Pacôme; Roux-Opstaele, Lutgart; Dreuillet, Caroline; Gonzalez-Marcano, Eglys; Millán, Olga; Jaeger, Ulrich; Delgado, Julio; Luu, Maik; Huber, Barbara; Lorrain, Margot; Pina, Mariana; Kremer, Andreas; Bolaños, Natacha; Clavreul, Solène; Nier, Samantha; Liu, Roberto D K; Lissenberg-Witte, Birgit I; Anguille, Sébastien; Robin, Marie; Morris, Emma C; Sureda, Anna; Préau, Marie; Pannard, Myriam; De Bock, Geertruida H; Wagers, Scott S; Negre, Hélène; Maucort-Boulch, Delphine; Hudecek, Michael; Uyl-de Groot, Carin A; Kersten, Marie José

Allogeneic hematopoietic stem cell transplantation outcome in oldest known surviving patients with Wiskott-Aldrich syndrome

已知最年长的Wiskott-Aldrich综合征存活患者接受异基因造血干细胞移植的预后

Anantharachagan, Ariharan; Loh, Sook Yin; Burns, Siobhan O; Laurence, Arian; Tadros, Susan; Tholouli, Eleni; Lwin, Yadanar; Martinez-Calle, Nicolas; Vaitla, P; Morris, Emma C

Humoral and cellular responses to SARS-CoV-2 in patients with B-cell haematological malignancies improve with successive vaccination

在患有B细胞血液系统恶性肿瘤的患者中,针对SARS-CoV-2的体液和细胞免疫反应会随着连续接种疫苗而改善。

Pinder, Christopher L; Jankovic, Dylan; Fox, Thomas A; Kirkwood, Amy; Enfield, Louise; Alrubayyi, Aljawharah; Touizer, Emma; Ford, Rosemarie; Pocock, Rachael; Shin, Jin-Sup; Ziegler, Joseph; Thomson, Kirsty J; Ardeshna, Kirit M; Peppa, Dimitra; McCoy, Laura E; Morris, Emma C

Practical challenges for functional validation of STAT1 gain of function genetic variants

STAT1功能获得性基因变异功能验证面临的实际挑战

Albuquerque, Adriana S; Maimaris, Jesmeen; McKenna, Alexander J; Lambourne, Jonathan; Moreira, Fernando; Workman, Sarita; Megy, Karyn; Simeoni, Ilenia; Lango Allen, Hana; Morris, Emma C; Burns, Siobhan O