Neural stem cells for disease modeling and evaluation of therapeutics for Tay-Sachs disease
神经干细胞用于疾病建模和 Tay-Sachs 病治疗评估
期刊:Orphanet Journal of Rare Diseases
影响因子:3.4
doi:10.1186/s13023-018-0886-3
Mylinh Vu, Rong Li, Amanda Baskfield, Billy Lu, Atena Farkhondeh, Kirill Gorshkov, Omid Motabar, Jeanette Beers, Guokai Chen, Jizhong Zou, Angela J Espejo-Mojica, Alexander Rodríguez-López, Carlos J Alméciga-Díaz, Luis A Barrera, Xuntian Jiang, Daniel S Ory, Juan J Marugan, Wei Zheng