International workshop: what is needed to ensure outcome measures for Rett syndrome are fit-for-purpose for clinical trials? June 7, 2023, Nashville, USA
国际研讨会:如何确保雷特综合征的疗效评价指标适用于临床试验?2023年6月7日,美国纳什维尔
期刊:Trials
影响因子:2
doi:10.1186/s13063-024-08678-6
Downs, Jenny; Pichard, Dominique C; Kaufmann, Walter E; Horrigan, Joseph P; Raspa, Melissa; Townend, Gillian; Marsh, Eric D; Leonard, Helen; Motil, Kathleen; Dietz, Andrew C; Garg, Nupur; Ananth, Amitha; Byiers, Breanne; Peters, Sarika; Beatty, Christopher; Symons, Frank; Jacobs, Aleksandra; Youakim, James; Suter, Bernhard; Santosh, Paramola; Neul, Jeffrey L; Benke, Tim A