日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Study of Testosterone and Recombinant Human Growth Hormone in Facioscapulohumeral Muscular Dystrophy

睾酮和重组人生长激素治疗面肩肱型肌营养不良症的研究

Heatwole, Chad Rydel; Luebbe, Elizabeth; Hamel, Johanna; Mongiovi, Phillip C; Ciafaloni, Emma; Dilek, Nuran; Martens, William B; Weber, David R; Rashid, Hani; Allen McKeown, Jamie; Smith, Claire H; Howell, Samantha; Rosero, Spencer Z; Eichinger, Katy; Baker, Lindsay S; Dekdebrun, Jeanne M; Hilbert, James E; Varma, Anika; Thornton, Charles A; McDermott, Michael P; Moxley, Richard T 3rd

Milestones of progression in myotonic dystrophy type 1 and type 2

1 型和 2 型强直性肌营养不良症的进展里程碑

Hamel, Johanna I; McDermott, Michael P; Hilbert, James E; Martens, William B; Luebbe, Elizabeth; Tawil, Rabi; Moxley, Richard T 3rd; Thornton, Charles A

Brief assessment of cognitive function in myotonic dystrophy: Multicenter longitudinal study using computer-assisted evaluation

肌强直性营养不良患者认知功能简要评估:一项采用计算机辅助评估的多中心纵向研究

Deutsch, Gayle K; Hagerman, Katharine A; Sampson, Jacinda; Dent, Gersham; Dekdebrun, Jeanne; Parker, Dana M; Thornton, Charles A; Heatwole, Chad R; Subramony, Sub H; Mankodi, Ami K; Ashizawa, Tetsuo; Statland, Jeffrey M; Arnold, W David; Moxley, Richard T 3rd; Day, John W

Consensus-based care recommendations for adults with myotonic dystrophy type 2

基于共识的2型强直性肌营养不良成人患者护理建议

Schoser, Benedikt; Montagnese, Federica; Bassez, Guillaume; Fossati, Barbara; Gamez, Josep; Heatwole, Chad; Hilbert, James; Kornblum, Cornelia; Kostera-Pruszczyk, Anne; Krahe, Ralf; Lusakowska, Anna; Meola, Giovanni; Moxley, Richard 3rd; Thornton, Charles; Udd, Bjarne; Formaker, Paul

Patient-reported study of the impact of pediatric-onset myotonic dystrophy

患者报告的儿童期发病强直性肌营养不良症影响研究

Hunter, Michael; Ekstrom, Anne-Berit; Campbell, Craig; Hung, Man; Bounsanga, Jerry; Bates, Kameron; Adams, Heather R; Luebbe, Elizabeth; Moxley, Richard T 3rd; Heatwole, Chad; Johnson, Nicholas E

Reproductive Cancer Risk Factors in Women With Myotonic Dystrophy (DM): Survey Data From the US and UK DM Registries

患有强直性肌营养不良症 (DM) 女性的生殖系统癌症风险因素:来自美国和英国 DM 登记处的调查数据

Higgs, Cecilia; Hilbert, James E; Wood, Libby; Martens, William B; Marini-Bettolo, Chiara; Nikolenko, Nikoletta; Alsaggaf, Rotana; Lochmüller, Hanns; Moxley, Richard T; Greene, Mark H; Wang, Youjin; Gadalla, Shahinaz M

Consensus-based care recommendations for adults with myotonic dystrophy type 1

针对1型强直性肌营养不良症成人患者的共识性护理建议

Ashizawa, Tetsuo; Gagnon, Cynthia; Groh, William J; Gutmann, Laurie; Johnson, Nicholas E; Meola, Giovanni; Moxley, Richard 3rd; Pandya, Shree; Rogers, Mark T; Simpson, Ericka; Angeard, Nathalie; Bassez, Guillaume; Berggren, Kiera N; Bhakta, Deepak; Bozzali, Marco; Broderick, Ann; Byrne, Janice L B; Campbell, Craig; Cup, Edith; Day, John W; De Mattia, Elisa; Duboc, Denis; Duong, Tina; Eichinger, Katy; Ekstrom, Anne-Berit; van Engelen, Baziel; Esparis, Belen; Eymard, Bruno; Ferschl, Marla; Gadalla, Shahinaz M; Gallais, Benjamin; Goodglick, Todd; Heatwole, Chad; Hilbert, James; Holland, Venessa; Kierkegaard, Marie; Koopman, Wilma J; Lane, Kari; Maas, Daphne; Mankodi, Ami; Mathews, Katherine D; Monckton, Darren G; Moser, David; Nazarian, Saman; Nguyen, Linda; Nopoulos, Peg; Petty, Richard; Phetteplace, Janel; Puymirat, Jack; Raman, Subha; Richer, Louis; Roma, Elisabetta; Sampson, Jacinda; Sansone, Valeria; Schoser, Benedikt; Sterling, Laurie; Statland, Jeffrey; Subramony, S H; Tian, Cuixia; Trujillo, Careniña; Tomaselli, Gordon; Turner, Chris; Venance, Shannon; Verma, Aparajitha; White, Molly; Winblad, Stefan

Paroxetine and fluconazole therapy for HIV-associated neurocognitive impairment: results from a double-blind, placebo-controlled trial.

帕罗西汀和氟康唑治疗 HIV 相关神经认知障碍:一项双盲、安慰剂对照试验的结果

Sacktor Ned, Skolasky Richard L, Moxley Richard, Wang Sheng, Mielke Michelle M, Munro Cynthia, Steiner Joseph, Nath Avindra, Haughey Norman, McArthur Justin

Efficacy and safety of deflazacort vs prednisone and placebo for Duchenne muscular dystrophy

地夫可特与泼尼松和安慰剂治疗杜氏肌营养不良症的疗效和安全性比较

Griggs, Robert C; Miller, J Phillip; Greenberg, Cheryl R; Fehlings, Darcy L; Pestronk, Alan; Mendell, Jerry R; Moxley, Richard T 3rd; King, Wendy; Kissel, John T; Cwik, Valerie; Vanasse, Michel; Florence, Julaine M; Pandya, Shree; Dubow, Jordan S; Meyer, James M

Parent-reported multi-national study of the impact of congenital and childhood onset myotonic dystrophy

一项由家长报告的多国研究,探讨了先天性和儿童期发病的强直性肌营养不良症的影响

Johnson, Nicholas E; Ekstrom, Anne-Berit; Campbell, Craig; Hung, Man; Adams, Heather R; Chen, Wei; Luebbe, Elizabeth; Hilbert, James; Moxley, Richard T 3rd; Heatwole, Chad R