日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

BCMA-directed mRNA CAR T cell therapy for myasthenia gravis: a randomized, double-blind, placebo-controlled phase 2b trial

BCMA靶向mRNA CAR T细胞疗法治疗重症肌无力:一项随机、双盲、安慰剂对照的2b期试验

Vu, Tuan; Durmus, Hacer; Rivner, Michael; Shroff, Sheetal; Ragole, Thomas; Myers, Bennett; Pasnoor, Mamatha; Small, George; Karam, Chafic; Vullaganti, Mithila; Peltier, Amanda; Sahagian, Gregory; Feinberg, Marc H; Slanksy, Adam; Barnett-Tapia, Carolina; Siddiqi, Zaeem; Gwathmey, Kelly; Badruddoja, Michael A; Kamboh, Hafsa; Ruggerie, Rachel N; Fedak, Renee R; Stewart, C Andrew; Kurtoglu, Metin; Kalayoglu, Murat; Singer, Michael; Jewell, Christopher M; Miljkovic, Milos D; Dimachkie, Mazen; Mozaffar, Tahseen; Howard, James F Jr

BCMA-directed mRNA CAR-T cell therapy for myasthenia gravis: exploratory biomarker analysis of a placebo-controlled phase 2b trial.

BCMA 靶向 mRNA CAR-T 细胞疗法治疗重症肌无力:安慰剂对照 2b 期试验的探索性生物标志物分析。

Fedak Renee R, Ruggerie Rachel N, Shan Yufei, Curvino Elizabeth J, de Sousa Juliana F, Daniel Shaji, Ngo-Casi Minhtran, Kamboh Hafsa, Vu Tuan, Durmuş Hacer, Mozaffar Tahseen, Howard James F Jr, English Emily P, Benson Albina, Duvernay Matthew T, Singer Michael S, Kalayoglu Murat V, Brunn Carsten, Bodansky Aaron, Anderson Mark S, DeRisi Joseph L, Garcia Samantha T, Yu David J L, Zorn Kelsey C, Kurtoglu Metin, Miljković Miloš D, Stewart C Andrew, Jewell Christopher M

Quantitative Measurement of Glycosylated ⍺-Dystroglycan as a Biomarker for Disease Severity in Limb-Girdle Muscular Dystrophy Type 2I/R9

定量测定糖基化α-肌营养不良蛋白聚糖作为肢带型肌营养不良症2I/R9型疾病严重程度的生物标志物

Vissing, John; Mozaffar, Tahseen; Johnson, Nicholas E; Mathews, Katherine D; Wicklund, Matthew P; Weihl, Conrad; Leung, Doris G; Statland, Jeffrey M; Kang, Peter B; Zingariello, Carla D; Lowes, Linda Pax; Desai, Urvi; Bates, Kameron; Alfano, Lindsay N; Xie, Han; St Romain, Jessica; Blankenbiller, Tricia; McLendon, George; Rajasingham, Thulashitha; Heitzer, Marjet; Wu-Zhang, Alyssa X; Tripp, Kenneth; Rodriguez, Hector M; Sproule, Douglas

Standardized Interoperable Data Collection for Myositis Research: Developing Expert Consensus on Common Data Elements for Myositis Outcome Measures

肌炎研究标准化互操作数据收集:就肌炎结局指标的通用数据元素达成专家共识

Saygin, Didem; Diller, Matthew; Surampudi, Varsha; Bodkin, Mark; Farhadi, Payam Noroozi; Mecoli, Christopher A; Kessel, Audrey; Aggarwal, Rohit; Alexanderson, Helene; Amato, Anthony; Bartels, Christie M; Benveniste, Olivier; Best, Michelle; Chinoy, Hector; de Groot, Ingrid; Feldman, Brian; Huber, Adam M; Kim, Hanna; Kim, Susan; Kobert, Linda; Leclair, Valerie; Lubinus, Manuel; Machado, Pedro M; Mammen, Andrew; McCann, Liza J; Mozaffar, Tahseen; Oddis, Chester; Paik, Julie J; Ravelli, Angelo; Ruperto, Nicolino; Schmidt, Jens; Werner, Ellen; Werth, Victoria; Schiffenbauer, Adam; Scheuermann, Richard H; Rider, Lisa G

Preliminary molecular detection of influenza RNA in synanthropic cockroaches from shiraz, Iran

伊朗设拉子地区与人类共生的蟑螂体内流感病毒RNA的初步分子检测

Kalantari, Mohsen; Vahedi, Mozaffar; Jamalidoust, Marzieh; Motevasel, Maryam; Hosseinpour, Amin

Eco-friendly mosquito control: Assessing the larvicidal and repellent effects of Dorema aucheri extract on Anopheles stephensi, the malaria vector

生态友好型蚊虫控制:评估多雷玛·奥切里提取物对疟疾媒介斯氏按蚊幼虫的杀灭和驱避效果

Hosseinpour, Amin; Vahedi, Mozaffar; Hamedi, Azadeh; Soltanian, Niloofar; Kazemi, Farnaz; Rezaee, Elham; Soltani, Aboozar

Economic and Demographic Factors Associated With Antenatal Care Utilization in Bangladesh: An Ordered Response Analysis Using Cross-Sectional Data

孟加拉国产前保健利用情况相关的经济和人口因素:基于横截面数据的有序响应分析

Sarkar, Shuvongkar; Kamruzzaman, Md; Khudri, Md Mohsan; Hosain, Md Mozaffar

Safety of home administration of cipaglucosidase alfa plus miglustat in late-onset Pompe disease: results from multiple clinical trials

居家使用西帕葡萄糖苷酶α联合米格鲁司他治疗晚发型庞贝病的安全性:多项临床试验的结果

Andersen, Henning; Díaz-Manera, Jordi; Goker-Alpan, Ozlem; Mozaffar, Tahseen; Sitaraman Das, Sheela; Fox, Brian; Amon, Farah; O'Brien-Prince, Kinesha; Goldman, Mitchell; Holdbrook, Fred; Jain, Vipul; Byrne, Barry J

Miglustat: a first-in-class enzyme stabilizer for cipaglucosidase alfa for the treatment of late-onset Pompe disease

米格鲁司他:一种用于治疗晚发型庞贝病的西帕葡萄糖苷酶α的首创酶稳定剂

Hopkin, Robert J; Byrne, Barry J; Dimachkie, Mazen M; Kishnani, Priya S; Mozaffar, Tahseen; Roberts, Mark; Schoser, Benedikt; van der Beek, Nadine A M E; van der Ploeg, Ans T; Wenninger, Stephan; Brudvig, Jon; Fox, Brian; Holdbrook, Fred; Jain, Vipul; Johnson, Franklin; Zhang, Jennifer; Parenti, Giancarlo

Analysis of Multilevel Factors Mobilizing the Spectrum of Interorganizational Knowledge Sharing for Facilitating Digital Transformation at Scale: Qualitative Study

影响组织间知识共享多层次因素以促进大规模数字化转型的定性研究

Mozaffar, Hajar; Williams, Robin; Cresswell, Kathrin