Precise Targeting of miRNA Sites Restores CFTR Activity in CF Bronchial Epithelial Cells
精准靶向 miRNA 位点可恢复 CF 支气管上皮细胞中的 CFTR 活性
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2020.02.001
De Santi, Chiara; Fernández Fernández, Elena; Gaul, Rachel; Vencken, Sebastian; Glasgow, Arlene; Oglesby, Irene K; Hurley, Killian; Hawkins, Finn; Mitash, Nilay; Mu, Fangping; Raoof, Rana; Henshall, David C; Cutrona, Meritxell B; Simpson, Jeremy C; Harvey, Brian J; Linnane, Barry; McNally, Paul; Cryan, Sally Ann; MacLoughlin, Ronan; Swiatecka-Urban, Agnieszka; Greene, Catherine M