日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

AAV基因疗法在重度B型血友病中持续发挥临床疗效

Reiss, Ulrike M; Davidoff, Andrew M; Tuddenham, Edward G D; Chowdary, Pratima; McIntosh, Jenny; Muczynski, Vincent; Journou, Malo; Simini, Giulia; Ireland, Lydia; Mohamed, Saira; Riddell, Anne; Pie, Arnulfo J; Hall, Andrew; Quaglia, Alberto; Mangles, Sarah; Mahlangu, Johnny; Haley, Kristina; Recht, Michael; Shen, Yu-Min; Halka, Kathleen G; Fortner, Gail; Morton, Christopher L; Gu, Zhengming; Hayden, Randall T; Neufeld, Ellis J; Okhomina, Victoria I; Kang, Guolian; Nathwani, Amit C

Consistent clinical factor VIII equivalency is unlikely for non-factor therapies in hemophilic mice

在血友病小鼠中,非因子疗法不太可能达到一致的临床因子VIII等效疗效。

Sefiane, Thibaud; McCluskey, Geneviève; Clavel, Marie; Maynadié, Hortense; Peyron, Ivan; David, Tovo; Brochier, Camille; Saller, François; Khamari, Mariem; Denis, Cécile V; Christophe, Olivier D; Lenting, Peter J; Muczynski, Vincent; Casari, Caterina

Erratum to: "Consistent clinical factor VIII equivalency is unlikely for non-factor therapies in hemophilic mice"

更正:“对于血友病小鼠的非因子疗法而言,不太可能出现一致的临床因子VIII等效性”

Sefiane, Thibaud; McCluskey, Geneviève; Clavel, Marie; Maynadié, Hortense; Peyron, Ivan; David, Tovo; Brochier, Camille; Saller, François; Khamari, Mariem; Denis, Cécile V; Christophe, Olivier D; Lenting, Peter J; Muczynski, Vincent; Casari, Caterina

Discovery of broad-spectrum antivirals targeting viral proteases using in silico structural modeling and cellular analysis

利用计算机结构建模和细胞分析发现靶向病毒蛋白酶的广谱抗病毒药物

Patel, Dharmeshkumar; De, Ramyani; Azadi, Niloufar; Lee, Sujin; Shooter, Savannah; Amichai, Sarah; Zhou, Shaoman; Monroe, Danielle; Mahanke, Cameron; McBrayer, Tamara R; Muczynski, Michael; Al-Homoudi, Abdullah; Engel, Joseph; Bochkov, Yury A; Gern, James E; Kovari, Ladislau C; Amblard, Franck; Schinazi, Raymond F

Human Structural Homologues of SARS-CoV-2 PL (pro) as Anti-Targets: A Strategic Panel Analysis

SARS-CoV-2 PL(pro) 的人类结构同源物作为抗靶点:一项战略性面板分析

Al-Homoudi, Abdullah I; Engel, Joseph; Muczynski, Michael D; Brunzelle, Joseph S; Gavande, Navnath S; Kovari, Ladislau C

Differences in venous clot structures between hemophilic mice treated with emicizumab versus factor VIII or factor VIIIFc

接受emicizumab治疗的血友病小鼠与接受因子VIII或因子VIIIFc治疗的血友病小鼠的静脉血栓结构存在差异

Sefiane, Thibaud; Maynadié, Hortense; Ettingshausen, Carmen Escurola; Muczynski, Vincent; Heiligenstein, Xavier; Dumont, Julien; Christophe, Olivier D; Denis, Cécile V; Casari, Caterina; Lenting, Peter J

Synthesis and biological evaluation of novel peptidomimetic inhibitors of the coronavirus 3C-like protease.

冠状病毒3C样蛋白酶新型肽模拟抑制剂的合成及生物学评价

Amblard Franck, LeCher Julia C, De Ramyani, Zhou Shaoman, Liu Peng, Goh Shu Ling, Tao Sijia, Patel Dharmeshkumar, Downs-Bowen Jessica, Zandi Keivan, Zhang Huanchun, Chaudhry Gitika, McBrayer Tamara, Muczynski Michael, Al-Homoudi Abdullah, Engel Joseph, Lan Shuiyun, Sarafianos Stefan G, Kovari Ladislau C, Schinazi Raymond F

Inducible localized delivery of an anti-PD-1 scFv enhances anti-tumor activity of ROR1 CAR-T cells in TNBC

诱导局部递送抗PD-1 scFv可增强ROR1 CAR-T细胞在三阴性乳腺癌中的抗肿瘤活性。

Micaela Harrasser ,Satyen Harish Gohil ,Hiu Lau ,Marco Della Peruta ,Vincent Muczynski ,Dominic Patel ,Elena Miranda ,Kristiana Grigoriadis ,Anita Grigoriadis ,David Granger ,Rachel Evans ,Amit Chunilal Nathwani

Neutrophil Activation and Neutrophil Extracellular Trap Formation in Dialysis Patients

透析患者的中性粒细胞活化和中性粒细胞胞外陷阱形成

Bieber, Scott; Muczynski, Kimberly A; Lood, Christian

Macrophage scavenger receptor SR-AI contributes to the clearance of von Willebrand factor

巨噬细胞清道夫受体SR-AI有助于清除血管性血友病因子

Wohner, Nikolett; Muczynski, Vincent; Mohamadi, Amel; Legendre, Paulette; Proulle, Valérie; Aymé, Gabriel; Christophe, Olivier D; Lenting, Peter J; Denis, Cécile V; Casari, Caterina