Dual AAV-based PCDH15 gene therapy achieves sustained rescue of visual function in a mouse model of Usher syndrome 1F
基于双 AAV 的 PCDH15 基因治疗在 Usher 综合征 1F 小鼠模型中实现了视觉功能的持续挽救
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2023.10.017
Sehar Riaz, Saumil Sethna, Todd Duncan, Muhammad A Naeem, T Michael Redmond, Sheikh Riazuddin, Saima Riazuddin, Livia S Carvalho, Zubair M Ahmed
