日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Durability of transgene expression after rAAV gene therapy

rAAV基因治疗后转基因表达的持久性

Muhuri, Manish; Levy, Daniel I; Schulz, Martin; McCarty, Douglas; Gao, Guangping

Overcoming innate immune barriers that impede AAV gene therapy vectors

克服阻碍AAV基因治疗载体的先天免疫屏障

Muhuri, Manish; Maeda, Yukiko; Ma, Hong; Ram, Sanjay; Fitzgerald, Katherine A; Tai, Phillip Wl; Gao, Guangping

Docosanoic acid conjugation to siRNA enables functional and safe delivery to skeletal and cardiac muscles.

将二十二碳酸与 siRNA 结合,可实现功能性且安全的递送至骨骼肌和心肌

Biscans Annabelle, Caiazzi Jillian, McHugh Nicholas, Hariharan Vignesh, Muhuri Manish, Khvorova Anastasia

Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens?

载体免疫疗法在传染病治疗中的应用:rAAV能否成为对抗传染性病原体的变革者?

Zhan, Wei; Muhuri, Manish; Tai, Phillip W L; Gao, Guangping