日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA

一种红细胞特异性慢病毒载体可改善XLSA新模型中的贫血和铁代谢。

Castruccio Castracani, Carlo; Breda, Laura; Papp, Tyler E; Guerra, Amaliris; Radaelli, Enrico; Assenmacher, Charles-Antoine; Finesso, Giovanni; Mui, Barbara L; Tam, Ying K; Fontana, Simona; Riganti, Chiara; Fiorito, Veronica; Petrillo, Sara; Tolosano, Emanuela; Parhiz, Hamideh; Rivella, Stefano

CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery

CD47肽包裹的脂质纳米颗粒促进细胞特异性mRNA递送

Papp, Tyler Ellis; Zeng, Jianhao; Shahnawaz, Hamna; Akyianu, Awurama; Breda, Laura; Yadegari, Amir; Steward, Joseph; Shi, Ruiqi; Li, Qin; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Rivella, Stefano; Shuvaev, Vladimir; Muzykantov, Vladimir R; Parhiz, Hamideh

Systemic delivery of biotherapeutic RNA to the myocardium transiently modulates cardiac contractility in vivo.

将生物治疗性 RNA 系统性输送至心肌可暂时性地调节体内心脏收缩力

Shuvaev Vladimir V, Tam Ying K, Lee Benjamin W, Myerson Jacob W, Herbst Alan, Kiseleva Raisa Yu, Glassman Patrick M, Parhiz Hamideh, Alameh Mohamad-Gabriel, Pardi Norbert, Muramatsu Hiromi, Shuvaeva Tea I, Arguiri Evguenia, Marcos-Contreras Oscar A, Hood Elizabeth D, Brysgel Taylor V, Nong Jia, Papp Tyler E, Eaton Deborah M, Riley Rachel, Palanki Rohan, Musunuru Kiran, Brenner Jacob S, Mitchell Michael J, Ferrari Victor A, Mui Barbara L, Semple Sean C, Weppler Sherry A, Atluri Pavan, Margulies Kenneth B, Weissman Drew, Muzykantov Vladimir R

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

利用靶向造血干细胞的脂质纳米颗粒构建致死性α-地中海贫血小鼠模型,并通过慢病毒基因治疗进行治疗。

Chappell, Maxwell E; Breda, Laura; Tricoli, Lucas; Guerra, Amaliris; Jarocha, Danuta; Castruccio Castracani, Carlo; Papp, Tyler E; Tanaka, Naoto; Hamilton, Nolan; Triebwasser, Michael P; Ghiaccio, Valentina; Fedorky, Megan T; Gollomp, Kandace L; Bochenek, Veronica; Roche, Aoife M; Everett, John K; Cook, Emma J; Bushman, Frederic D; Teawtrakul, Nattiya; Glentis, Stavros; Kattamis, Antonis; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Abdulmalik, Osheiza; Parhiz, Hamideh; Rivella, Stefano

Targeting lipid nanoparticles to the blood-brain barrier to ameliorate acute ischemic stroke

将脂质纳米颗粒靶向血脑屏障以改善急性缺血性卒中

Nong, Jia; Glassman, Patrick M; Shuvaev, Vladimir V; Reyes-Esteves, Sahily; Descamps, Helene C; Kiseleva, Raisa Y; Papp, Tyler E; Alameh, Mohamad-Gabriel; Tam, Ying K; Mui, Barbara L; Omo-Lamai, Serena; Zamora, Marco E; Shuvaeva, Tea; Arguiri, Evguenia; Gong, Xijing; Brysgel, Taylor V; Tan, Ai Wen; Woolfork, Ashley G; Weljie, Aalim; Thaiss, Christoph A; Myerson, Jacob W; Weissman, Drew; Kasner, Scott E; Parhiz, Hamideh; Muzykantov, Vladimir R; Brenner, Jacob S; Marcos-Contreras, Oscar A

In vivo hematopoietic stem cell modification by mRNA delivery

通过mRNA递送对体内造血干细胞进行修饰

Breda, Laura; Papp, Tyler E; Triebwasser, Michael P; Yadegari, Amir; Fedorky, Megan T; Tanaka, Naoto; Abdulmalik, Osheiza; Pavani, Giulia; Wang, Yongping; Grupp, Stephan A; Chou, Stella T; Ni, Houping; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Rivella, Stefano; Parhiz, Hamideh

Targeting lipid nanoparticles to the blood brain barrier to ameliorate acute ischemic stroke

将脂质纳米颗粒靶向血脑屏障以改善急性缺血性卒中

Nong, Jia; Glassman, Patrick M; Reyes-Esteves, Sahily; Descamps, Helene C; Shuvaev, Vladimir V; Kiseleva, Raisa Y; Papp, Tyler E; Alameh, Mohamad-Gabriel; Tam, Ying K; Mui, Barbara L; Omo-Lamai, Serena; Zamora, Marco E; Shuvaeva, Tea; Arguiri, Evguenia; Thaiss, Christoph A; Myerson, Jacob W; Weissman, Drew; Kasner, Scott E; Parhiz, Hamideh; Muzykantov, Vladimir R; Brenner, Jacob S; Marcos-Contreras, Oscar A

CAR T cells produced in vivo to treat cardiac injury

体内产生的CAR-T细胞用于治疗心脏损伤

Rurik, Joel G; Tombácz, István; Yadegari, Amir; Méndez Fernández, Pedro O; Shewale, Swapnil V; Li, Li; Kimura, Toru; Soliman, Ousamah Younoss; Papp, Tyler E; Tam, Ying K; Mui, Barbara L; Albelda, Steven M; Puré, Ellen; June, Carl H; Aghajanian, Haig; Weissman, Drew; Parhiz, Hamideh; Epstein, Jonathan A

Lipid nanoparticles enhance the efficacy of mRNA and protein subunit vaccines by inducing robust T follicular helper cell and humoral responses

脂质纳米颗粒通过诱导强烈的滤泡辅助性T细胞和体液免疫反应,增强mRNA和蛋白质亚单位疫苗的疗效。

Alameh, Mohamad-Gabriel; Tombácz, István; Bettini, Emily; Lederer, Katlyn; Sittplangkoon, Chutamath; Wilmore, Joel R; Gaudette, Brian T; Soliman, Ousamah Y; Pine, Matthew; Hicks, Philip; Manzoni, Tomaz B; Knox, James J; Johnson, John L; Laczkó, Dorottya; Muramatsu, Hiromi; Davis, Benjamin; Meng, Wenzhao; Rosenfeld, Aaron M; Strohmeier, Shirin; Lin, Paulo J C; Mui, Barbara L; Tam, Ying K; Karikó, Katalin; Jacquet, Alain; Krammer, Florian; Bates, Paul; Cancro, Michael P; Weissman, Drew; Luning Prak, Eline T; Allman, David; Locci, Michela; Pardi, Norbert

Selective targeting of nanomedicine to inflamed cerebral vasculature to enhance the blood-brain barrier

将纳米药物选择性靶向输送至发炎的脑血管,以增强血脑屏障

Marcos-Contreras, Oscar A; Greineder, Colin F; Kiseleva, Raisa Yu; Parhiz, Hamideh; Walsh, Landis R; Zuluaga-Ramirez, Viviana; Myerson, Jacob W; Hood, Elizabeth D; Villa, Carlos H; Tombacz, Istvan; Pardi, Norbert; Seliga, Alecia; Mui, Barbara L; Tam, Ying K; Glassman, Patrick M; Shuvaev, Vladimir V; Nong, Jia; Brenner, Jacob S; Khoshnejad, Makan; Madden, Tom; Weissmann, Drew; Persidsky, Yuri; Muzykantov, Vladimir R