Oral cysteamine bitartrate and N-acetylcysteine for patients with infantile neuronal ceroid lipofuscinosis: a pilot study
口服酒石酸半胱胺和N-乙酰半胱氨酸治疗婴儿神经元蜡样脂褐质沉积症:一项初步研究
期刊:Lancet Neurology
影响因子:45.5
doi:10.1016/S1474-4422(14)70142-5
Levin, Sondra W; Baker, Eva H; Zein, Wadih M; Zhang, Zhongjian; Quezado, Zenaide M N; Miao, Ning; Gropman, Andrea; Griffin, Kurt J; Bianconi, Simona; Chandra, Goutam; Khan, Omar I; Caruso, Rafael C; Liu, Aiyi; Mukherjee, Anil B