日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cooperative supramolecular integration of QS-21 into polymeric micelles as a tunable nanoadjuvant platform for subunit vaccines

将QS-21协同超分子整合到聚合物胶束中,作为亚单位疫苗的可调控纳米佐剂平台

Ward, Kailee S; Ptak, Christopher P; Pashkova, Natalya; Grider, Tiffany; Peterson, Tabitha A; Pareyson, Davide; Pisciotta, Chiara; Saveri, Paola; Moroni, Isabella; Laura, Matilde; Burns, Joshua; Menezes, Manoj P; Cornett, Kayla; Finkel, Richard; Mukherjee-Clavin, Bipasha; Sumner, Charlotte J; Greene, Maxwell; Abdul Hamid, Omer; Herrmann, David; Sadjadi, Reza; Walk, David; Züchner, Stephan; Reilly, Mary M; Scherer, Steven S; Piper, Robert C; Shy, Michael E; Márquez, Patricio Guillermo; Alonso, Leonardo Gabriel; Marfía, Juan Ignacio; Smith, Ignacio; Mourelle, Ana Carolina; Formica, María Lina; Miranda, María Victoria; Valdez, Silvina Noemí; Wolman, Federico Javier; Glisoni, Romina Julieta

Charcot-Marie-Tooth disease type 1E: Clinical Natural History and Molecular Impact of PMP22 Variants

夏科-马里-图斯病1E型:临床自然史和PMP22变异的分子影响

Ward, Kailee S; Ptak, Christopher P; Pashkova, Natalya; Grider, Tiffany; Peterson, Tabitha A; Pareyson, Davide; Pisciotta, Chiara; Saveri, Paola; Moroni, Isabella; Laura, Matilde; Burns, Joshua; Menezes, Manoj P; Cornett, Kayla; Finkel, Richard; Mukherjee-Clavin, Bipasha; Sumner, Charlotte J; Greene, Maxwell; Hamid, Omer Abdul; Herrmann, David; Sadjadi, Reza; Walk, David; Züchner, Stephan; Reilly, Mary M; Scherer, Steven S; Piper, Robert C; Shy, Michael E

Advances and challenges in modeling inherited peripheral neuropathies using iPSCs

利用诱导多能干细胞构建遗传性周围神经病模型的研究进展与挑战

Van Lent, Jonas; Prior, Robert; Pérez Siles, Gonzalo; Cutrupi, Anthony N; Kennerson, Marina L; Vangansewinkel, Tim; Wolfs, Esther; Mukherjee-Clavin, Bipasha; Nevin, Zachary; Judge, Luke; Conklin, Bruce; Tyynismaa, Henna; Clark, Alex J; Bennett, David L; Van Den Bosch, Ludo; Saporta, Mario; Timmerman, Vincent

hESC- and hiPSC-derived Schwann cells are molecularly comparable and functionally equivalent

人胚胎干细胞(hESC)和人诱导多能干细胞(hiPSC)衍生的雪旺细胞在分子水平上具有可比性,功能上也等效。

Kathryn R Moss,Ruifa Mi,Riki Kawaguchi,Jeffrey T Ehmsen,Qiang Shi,Paula I Vargas,Bipasha Mukherjee-Clavin,Gabsang Lee

Comparison of three congruent patient-specific cell types for the modelling of a human genetic Schwann-cell disorder

比较三种一致的患者特异性细胞类型,用于构建人类遗传性雪旺细胞疾病模型

Bipasha Mukherjee-Clavin ,Ruifa Mi ,Barbara Kern ,In Young Choi ,Hotae Lim ,Yohan Oh ,Benjamin Lannon ,Kevin J Kim ,Shaughn Bell ,Junho K Hur ,Woochang Hwang ,Young Hyun Che ,Omer Habib ,Robert H Baloh ,Kevin Eggan ,Gerald Brandacher ,Ahmet Hoke ,Lorenz Studer ,Yong Jun Kim ,Gabsang Lee

Large-scale screening using familial dysautonomia induced pluripotent stem cells identifies compounds that rescue IKBKAP expression

利用家族性自主神经功能障碍诱导的多能干细胞进行大规模筛选,鉴定出能够挽救 IKBKAP 表达的化合物。

Lee, Gabsang; Ramirez, Christina N; Kim, Hyesoo; Zeltner, Nadja; Liu, Becky; Radu, Constantin; Bhinder, Bhavneet; Kim, Yong Jun; Choi, In Young; Mukherjee-Clavin, Bipasha; Djaballah, Hakim; Studer, Lorenz