日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients with Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial

Delandistrogene Moxeparvovec 治疗可活动杜氏肌营养不良症患者的两年疗效：3 期 EMBARK 试验

期刊:Neurology and Therapy
影响因子:4.8
doi:10.1007/s40120-025-00879-8
Mendell, Jerry R; Muntoni, Francesco; McDonald, Craig M; Mercuri, Eugenio M; Ciafaloni, Emma; Komaki, Hirofumi; Leon-Astudillo, Carmen; Nascimento, Andrés; Proud, Crystal; Schara-Schmidt, Ulrike; Veerapandiyan, Aravindhan; Zaidman, Craig M; Furgerson, Matthew; Ding, Kai; Singh, Preeti; Potter, Rachael; Asher, Damon R; Murphy, Alexander P; Reid, Carol; Hooper, Gregory; Torre, Carmen O; Manfrini, Marianna; Rodino-Klapac, Louise R
发表日期：2026
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AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

AAV基因疗法治疗杜氏肌营养不良症：EMBARK 3期随机试验

期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-024-03304-z
Mendell Jerry R, Muntoni Francesco, McDonald Craig M, Mercuri Eugenio M, Ciafaloni Emma, Komaki Hirofumi, Leon-Astudillo Carmen, Nascimento Andrés, Proud Crystal, Schara-Schmidt Ulrike, Veerapandiyan Aravindhan, Zaidman Craig M, Guridi Maitea, Murphy Alexander P, Reid Carol, Wandel Christoph, Asher Damon R, Darton Eddie, Mason Stefanie, Potter Rachael A, Singh Teji, Zhang Wenfei, Fontoura Paulo, Elkins Jacob S, Rodino-Klapac Louise R
其它
发表日期：2025
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Quantitative Muscle Magnetic Resonance Outcomes in Patients With Duchenne Muscular Dystrophy: An Exploratory Analysis From the EMBARK Randomized Clinical Trial

杜氏肌营养不良症患者的定量肌肉磁共振结果：来自 EMBARK 随机临床试验的探索性分析

期刊:Jama Neurology
影响因子:21.3
doi:10.1001/jamaneurol.2025.0992
Vandenborne, Krista; Walter, Glenn A; Straub, Volker; Willcocks, Rebecca J; Forbes, Sean C; Mercuri, Eugenio M; Muntoni, Francesco; Ding, Kai; Ennamuri, Sravya; Reid, Carol; Murphy, Alexander P; Manfrini, Marianna; Mendell, Jerry R; Elkins, Jacob S; Rodino-Klapac, Louise R
发表日期：2025
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Exploring the natural history of bone mineral density in Duchenne muscular dystrophy: a systematic literature review

探索杜氏肌营养不良症患者骨矿物质密度的自然史：系统性文献综述

期刊:Osteoporosis International
影响因子:5.4
doi:10.1007/s00198-025-07651-6
De Ford, Christian; Guridi, Maitea; Chen, Yingjia; Murphy, Alexander P; Wood, Claire; McMillan, Hugh J; Mercuri, Eugenio; Crabtree, Nicola; Ward, Leanne
发表日期：2025
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Caregiver Global Impression Observations from EMBARK: A Phase 3 Study Evaluating Delandistrogene Moxeparvovec in Ambulatory Patients with Duchenne Muscular Dystrophy

来自 EMBARK 的照护者总体印象观察：一项评估 Delandistrogene Moxeparvovec 对可活动杜氏肌营养不良症患者的 3 期研究

期刊:Neurology and Therapy
影响因子:4.8
doi:10.1007/s40120-024-00685-8
McDonald, Craig M; Elkins, Jacob S; Dharmarajan, Sai; Gooch, Katherine; Ciobanu, Teofil; Lansdall, Claire J; Murphy, Alexander P; McDougall, Fiona; Mercuri, Eugenio M; Audhya, Ivana
发表日期：2025
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Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy

对接受 delandistrogene moxeparvovec 基因治疗后发生的转基因导向免疫介导性肌炎进行免疫学研究

期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-024-84077-w
Potter, Rachael A; Moeller, Ida H; Khan, Sohrab; Haegel, Hélène; Hollenstein, Andreas; Steiner, Guido; Wandel, Christoph; Murphy, Alexander P; Asher, Damon R; Palatinsky, Emanuel; Griffin, Danielle A; Mason, Stefanie; Iannaccone, Susan T; Zaidman, Craig M; Rodino-Klapac, Louise R
基因治疗
免疫/内分泌
发表日期：2025
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A patient-centered qualitative evaluation of meaningful change on the NSAA and PUL in Duchenne Muscular Dystrophy

以患者为中心的杜氏肌营养不良症患者NSAA和PUL评分有意义变化的定性评估

期刊:Frontiers in Neurology
影响因子:2.8
doi:10.3389/fneur.2025.1509174
Gillman, Aviva; Ciobanu, Teofil; Barrett, Louise; Davies, Evan W; Murphy, Alexander P; Johnson, Alex; Mills, Jessica; Heinrich, Phoebe; Przydzial, Krystian; Ewens, Bethany; Vandenberg, Gerrit; Cano, Stefan; Mayhew, Anna
发表日期：2025
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Designing and interpreting 4D tumour spheroid experiments

设计和解释 4D 肿瘤球体实验

期刊:Communications Biology
影响因子:5.2
doi:10.1038/s42003-022-03018-3
Ryan J Murphy, Alexander P Browning, Gency Gunasingh, Nikolas K Haass #, Matthew J Simpson #
肿瘤
发表日期：2022
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Natural history of limb girdle muscular dystrophy R9 over 6 years: searching for trial endpoints

肢带型肌营养不良症R9 6年自然史：寻找试验终点

期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.774
Murphy, Alexander P; Morrow, Jasper; Dahlqvist, Julia R; Stojkovic, Tanya; Willis, Tracey A; Sinclair, Christopher D J; Wastling, Stephen; Yousry, Tarek; Hanna, Michael S; James, Meredith K; Mayhew, Anna; Eagle, Michelle; Lee, Laurence E; Hogrel, Jean-Yves; Carlier, Pierre G; Thornton, John S; Vissing, John; Hollingsworth, Kieren G; Straub, Volker
发表日期：2019
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