日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A CRISPR-Cas13d cancer therapeutic enables selective elimination of uveal melanoma

一种 CRISPR-Cas13d 癌症疗法能够选择性地消除葡萄膜黑色素瘤

Stauber, Daniel; Sosnick, Lucas; Ma, Yitong; Pimcharoen, Sopida; Lawanprasert, Atip; Murthy, Niren; Myung, David; Qi, Lei S

Recent developments in the delivery of peptide nucleic acids (PNAs)

肽核酸(PNA)递送技术的最新进展

Sarkar, Srijani; Murthy, Niren

Multiplexed epigenetic memory editing using CRISPRoff sensitizes glioblastoma to chemotherapy.

利用 CRISPRoff 进行多重表观遗传记忆编辑可增强胶质母细胞瘤对化疗的敏感性

Lin Katie, Zou Christopher, Hubbard Akane, Sengelmann Sasha, Goudy Laine, Wang I-Ching, Sharma Rohit, Pak Joanna, Foster Kyla, Ozawa Tomoko, de Groot John F, Phillips Joanna, Vasudevan Harish N, Raleigh David R, Marson Alexander, Murthy Niren, Gilbert Luke A, Berger Mitchel S, Liu S John

Advances in acid-degradable and enzyme-cleavable linkers for drug delivery

用于药物递送的酸降解和酶裂解连接子的研究进展

Zhao, Sheng; Yu, Na; Han, Hesong; Guo, Shutao; Murthy, Niren

Correction: Identification of acrylamide-based covalent inhibitors of SARS-CoV-2 (SCoV-2) Nsp15 using high-throughput screening and machine learning

更正:利用高通量筛选和机器学习鉴定基于丙烯酰胺的SARS-CoV-2 (SCoV-2) Nsp15共价抑制剂

Bajaj, Teena; Mosavati, Babak; Zhang, Lydia H; Parsa, Mohammad S; Wang, Huanchen; Kerek, Evan M; Liang, Xueying; Tabatabaei Dakhili, Seyed Amir; Wehri, Eddie; Guo, Silin; Desai, Rushil N; Orr, Lauren M; Mofrad, Mohammad R K; Schaletzky, Julia; Ussher, John R; Deng, Xufang; Stanley, Robin; Hubbard, Basil P; Nomura, Daniel K; Murthy, Niren

Identification of acrylamide-based covalent inhibitors of SARS-CoV-2 (SCoV-2) Nsp15 using high-throughput screening and machine learning.

利用高通量筛选和机器学习鉴定 SARS-CoV-2 (SCoV-2) Nsp15 的丙烯酰胺基共价抑制剂

Bajaj Teena, Mosavati Babak, Zhang Lydia H, Parsa Mohammad S, Wang Huanchen, Kerek Evan M, Liang Xueying, Tabatabaei Dakhili Seyed Amir, Wehri Eddie, Guo Silin, Desai Rushil N, Orr Lauren M, Mofrad Mohammad R K, Schaletzky Julia, Ussher John R, Deng Xufang, Stanley Robin, Hubbard Basil P, Nomura Daniel K, Murthy Niren

Synthesis, radiolabeling, and biological evaluation of methyl 6-deoxy-6-[(18)F]fluoro-4-thio-α-d-maltotrioside as a positron emission tomography bacterial imaging agent.

甲基 6-脱氧-6-[(18)F]氟-4-硫代-α-D-麦芽三糖苷作为正电子发射断层扫描细菌成像剂的合成、放射性标记和生物学评价

Takemiya Kiyoko, Seo Wonewoo, Voll Ronald J, Zhao Sheng, Joseph Giji, Wang Shelly, Zeng Fanxing, Nye Jonathon A, Murthy Niren, Taylor W Robert, Goodman Mark M

Efficient in vivo mammalian neuron editing using peptide-mediated CRISPR enzyme delivery

利用肽介导的CRISPR酶递送实现高效的体内哺乳动物神经元编辑

Manohar, Brigette D; Travis, Meika; Munjal, Vikas; Baehr, Christopher M; Rahnama, Lily M A; Kang, Min Hyung; Haddad, Rania F; Asija, Kunica; Noel, Eric A; Peddireddy, Navya; Chouhan, Runvir S; Sharma, Rohit; Wyman, Stacia K; Krishnappa, Netravathi; Killebrew, Deirdre A; Li, Song Hua; Snow, Kathy J; Byrne, Addison K; Boosani, Chandra S; Otero, P Anthony; Bringas, John; O'Brien, Allison A; Rocco, Matthew T; Zimmerly, Madison P; Gray, Isabelle; Sran, Gunita K; Patel, Mia I; Seidensticker, Emily F; Saville, Ethan; Gaitan, Yaned; Schmelzle, Amanda L; Subramanyam, Pradeep Nag B; Samaranch, Lluis; Green, Jonathan A; Wells, Kevin D; Ehrenberg, Alexander J; Murray, Stephen A; Clelland, Claire D; Murthy, Niren; Lonser, Russell R; Hadaczek, Piotr; Van Laar, Victor S; Bankiewicz, Krystof S; Wilson, Ross C

CRISPR-Cas13d-Mediated Targeting of a Context-Specific Essential Gene Enables Selective Elimination of Uveal Melanoma

利用 CRISPR-Cas13d 介导的靶向特定背景必需基因可选择性消除葡萄膜黑色素瘤

Stauber, Daniel; Sosnick, Lucas; Ma, Yitong; Pimcharoen, Sopida; Lawanprasert, Atip; Murthy, Niren; Myung, David; Qi, Lei Stanley

Swine reporter model for preclinical evaluation and characterization of gene delivery vectors.

猪报告基因模型用于基因递送载体的临床前评价和表征

Campbell Jarryd M, Korpela Derek M, Han Hesong, Zhao Sheng, Webster Dennis A, Nguyen Yen Anh H, Aune Robyn O, Dagan Hinsoukpo, Milliken Rebecca, Watts Jonathan K, Murthy Niren, Carlson Daniel F