CTx001 for Geographic Atrophy: A Gene Therapy Expressing Soluble, Truncated Complement Receptor 1 (Mini-CR1)
CTx001 用于治疗地图状萎缩:一种表达可溶性截短补体受体 1 (Mini-CR1) 的基因疗法
期刊:Ophthalmology Science
影响因子:4.6
doi:10.1016/j.xops.2025.100980
Rathi, Sonika; Didangelos, Athanasios; Pisarenka, Sofiya; Green, Rachel; Zafeiri, Stamatia; Emery-Billcliff, Peter; Patel, Nakul; Whalley, Pamela; Zamiri, Parisa; Tilakaratna, Viranga; Szula, Ewa; Hasan, Rafiq; Munye, Mustafa M; Unwin, Richard D; Bishop, Paul N; Keefe, Dennis; Clark, Simon J