日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV: An Overview of Unanswered Questions

AAV:未解之谜概述

Berns, Kenneth I; Muzyczka, Nicholas

Mutants at the 2-Fold Interface of Adeno-associated Virus Type 2 (AAV2) Structural Proteins Suggest a Role in Viral Transcription for AAV Capsids

腺相关病毒2型(AAV2)结构蛋白双折叠界面处的突变体表明其在AAV衣壳的病毒转录中发挥作用

Aydemir, Fikret; Salganik, Maxim; Resztak, Justyna; Singh, Jasbir; Bennett, Antonette; Agbandje-McKenna, Mavis; Muzyczka, Nicholas

Adeno-Associated Virus Type 2 and Hepatocellular Carcinoma?

腺相关病毒2型与肝细胞癌?

Berns, Kenneth I; Byrne, Barry J; Flotte, Terence R; Gao, Guangping; Hauswirth, William W; Herzog, Roland W; Muzyczka, Nicholas; VandenDriessche, Thierry; Xiao, Xiao; Zolotukhin, Sergei; Srivastava, Arun

Enhanced transgene expression from recombinant single-stranded D-sequence-substituted adeno-associated virus vectors in human cell lines in vitro and in murine hepatocytes in vivo

体外人细胞系和体内小鼠肝细胞中,重组单链D序列取代腺相关病毒载体的转基因表达增强

Ling, Chen; Wang, Yuan; Lu, Yuan; Wang, Lina; Jayandharan, Giridhara R; Aslanidi, George V; Li, Baozheng; Cheng, Binbin; Ma, Wenqin; Lentz, Thomas; Ling, Changquan; Xiao, Xiao; Samulski, R Jude; Muzyczka, Nicholas; Srivastava, Arun

Adeno-associated virus serotype 1 (AAV1)- and AAV5-antibody complex structures reveal evolutionary commonalities in parvovirus antigenic reactivity

腺相关病毒1型(AAV1)和AAV5抗体复合物的结构揭示了细小病毒抗原反应性的进化共性

Tseng, Yu-Shan; Gurda, Brittney L; Chipman, Paul; McKenna, Robert; Afione, Sandra; Chiorini, John A; Muzyczka, Nicholas; Olson, Norman H; Baker, Timothy S; Kleinschmidt, Jürgen; Agbandje-McKenna, Mavis

OneBac: platform for scalable and high-titer production of adeno-associated virus serotype 1-12 vectors for gene therapy

OneBac:用于基因治疗的腺相关病毒1-12型载体可扩展、高滴度生产的平台

Mietzsch, Mario; Grasse, Sabrina; Zurawski, Catherine; Weger, Stefan; Bennett, Antonette; Agbandje-McKenna, Mavis; Muzyczka, Nicholas; Zolotukhin, Sergei; Heilbronn, Regine

Structure and dynamics of adeno-associated virus serotype 1 VP1-unique N-terminal domain and its role in capsid trafficking

腺相关病毒1型VP1特有N端结构域的结构和动力学及其在衣壳运输中的作用

Venkatakrishnan, Balasubramanian; Yarbrough, Joseph; Domsic, John; Bennett, Antonette; Bothner, Brian; Kozyreva, Olga G; Samulski, R Jude; Muzyczka, Nicholas; McKenna, Robert; Agbandje-McKenna, Mavis

Structural insights into adeno-associated virus serotype 5

腺相关病毒5型血清型的结构解析

Govindasamy, Lakshmanan; DiMattia, Michael A; Gurda, Brittney L; Halder, Sujata; McKenna, Robert; Chiorini, John A; Muzyczka, Nicholas; Zolotukhin, Sergei; Agbandje-McKenna, Mavis

Capsid antibodies to different adeno-associated virus serotypes bind common regions

针对不同腺相关病毒血清型的衣壳抗体结合共同区域

Gurda, Brittney L; DiMattia, Michael A; Miller, Edward B; Bennett, Antonette; McKenna, Robert; Weichert, Wendy S; Nelson, Christian D; Chen, Wei-jun; Muzyczka, Nicholas; Olson, Norman H; Sinkovits, Robert S; Chiorini, John A; Zolotutkhin, Sergei; Kozyreva, Olga G; Samulski, R Jude; Baker, Timothy S; Parrish, Colin R; Agbandje-McKenna, Mavis

Structural insight into the unique properties of adeno-associated virus serotype 9

对腺相关病毒9型血清型独特特性的结构性见解

DiMattia, Michael A; Nam, Hyun-Joo; Van Vliet, Kim; Mitchell, Matthew; Bennett, Antonette; Gurda, Brittney L; McKenna, Robert; Olson, Norman H; Sinkovits, Robert S; Potter, Mark; Byrne, Barry J; Aslanidi, George; Zolotukhin, Sergei; Muzyczka, Nicholas; Baker, Timothy S; Agbandje-McKenna, Mavis