Suppression of autophagy permits successful enzyme replacement therapy in a lysosomal storage disorder--murine Pompe disease
抑制自噬可使溶酶体贮积症(小鼠庞贝病)的酶替代疗法取得成功。
期刊:Autophagy
影响因子:14.6
doi:10.4161/auto.6.8.13378
Nina Raben ,Cynthia Schreiner, Rebecca Baum, Shoichi Takikita, Sengen Xu, Tao Xie, Rachel Myerowitz, Masaaki Komatsu, Jack H Van der Meulen, Kanneboyina Nagaraju, Evelyn Ralston, Paul H Plotz