日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Charting the translational pathway: ISSCR best practices for the development of PSC-derived therapies

规划转化路径:ISSCR关于PSC衍生疗法开发的最佳实践

Barry, Jacqueline; Abranches, Elsa; Baptista, Ricardo P; Barry, Chris; Brandsten, Catharina; Bruce, Kevin; Carpenter, Melissa K; Cavagnaro, Joy; Collins, Lila; Csaszar, Elizabeth; Dashnau, Jennifer; de Villa, Denise; Fynes, Kate; Gabaldo, Michela; Hao, Jie; Harel-Adar, Tamar; Hei, Derek; Henchcliffe, Claire; Hidalgo-Simon, Ana; Hollands, Jennifer; Hursh, Deborah; Jackman, Shawna; Kelly, Kilian; Kim, Jung-Hyun; Kim, Hyunyoung; Kino-Oka, Masahiro; Lakshmipathy, Uma; Lamb, Tyler; Lazic, Stanley E; Loring, Jeanne F; Ludwig, Tenneille E; Mariappan, Indumathi; Monville, Christelle; Mountford, Joanne C; Nagy, Andras; Okano, Hideyuki; Pellegrini, Graziella; Persson, Annelie; Prutton, Kendra; Rasko, John E J; Sareen, Dhruv; Sato, Yoji; Shnaiderman, Anat; Stacey, Glyn; Svendsen, Clive N; Tomishima, Mark; Trounson, Alan; Viswanathan, Sowmya; Wang, Shuyan; Wydenbach, Kirsty; Zhang, Alex; Zylberberg, Claudia; Mosher, Jack T; Bharti, Kapil

Genome-edited safe and immune-evasive human pluripotent cells: Potential solution for allogeneic therapies.

基因编辑的安全且免疫逃逸的人类多能干细胞:同种异体疗法的潜在解决方案。

Tam Vivian, Wong Nicole Ching Man, Poon Andrew Chung Hin, Zhu Mengxia, Mei Ting, Kwok Janette, Chu Patrick, Jong Eric D, Tang Jean Kit, Nagy Andras, Chan Danny

GDF11-secreting cell transplant efficiently ameliorates age-related pulmonary fibrosis

分泌GDF11的细胞移植可有效改善与年龄相关的肺纤维化

Guo, Li; Duchesneau, Pascal; Jong, Eric D; Sawula, Evan; Li, Chengjin; Waddell, Thomas K; Nagy, Andras

Substrate stiffness dictates unique doxorubicin-induced senescence-associated secretory phenotypes and transcriptomic signatures in human pulmonary fibroblasts.

基质硬度决定了人类肺成纤维细胞中独特的阿霉素诱导衰老相关分泌表型和转录组特征

Du Huixun, Rose Jacob P, Bons Joanna, Guo Li, Valentino Taylor R, Wu Fei, Burton Jordan B, Basisty Nathan, Manwaring-Mueller Max, Makhijani Priya, Chen Nan, Chang Veronica, Winer Shawn, Campisi Judith, Furman David, Nagy Andras, Schilling Birgit, Winer Daniel A

Engineered mesenchymal stromal cells with interleukin-1beta sticky-trap attenuate osteoarthritis in knee joints.

经基因工程改造的间充质干细胞,利用白细胞介素-1β粘性陷阱,可减轻膝关节骨关节炎

Kim Christopher, Li Biao, Nakamura Sayaka, Neely Eric J, Rockel Jason S, Oussenko Tatiana, Zhang Puzheng, Kapoor Mohit, Nagy Andras

Tolerability and Safety of Large-Volume Hyaluronidase-Facilitated Subcutaneous Immunoglobulin 10% Administered with or without Dose Ramp-Up: A Phase 1 Study in Healthy Participants

大剂量透明质酸酶辅助皮下注射10%免疫球蛋白(有或无剂量递增)的耐受性和安全性:一项针对健康受试者的1期研究

Li, Zhaoyang; Nagy, Andras; Lindner, Dirk; Duff, Kim; Garcia, Enrique; Ay, Hakan; Rondon, Juan Carlos; Yel, Leman

Long-Term Safety of Facilitated Subcutaneous Immunoglobulin 10% Treatment in US Clinical Practice in Patients with Primary Immunodeficiency Diseases: Results from a Post-Authorization Safety Study

在美国临床实践中,皮下注射10%免疫球蛋白辅助治疗原发性免疫缺陷病患者的长期安全性:一项上市后安全性研究的结果

Rubinstein, Arye; Mabudian, Mohsen; McNeil, Donald; Patel, Niraj C; Wasserman, Richard L; Gupta, Sudhir; Carrasco, Paz; Chen, Jie; Garcia, Enrique; Nagy, Andras; Yel, Leman

A Phase 1 Open-Label Study to Assess the Tolerability, Safety, and Immunogenicity of Hyaluronidase-Facilitated Subcutaneous Immunoglobulin 20% in Healthy Adults

一项评估透明质酸酶辅助皮下注射20%免疫球蛋白在健康成人中耐受性、安全性和免疫原性的1期开放标签研究

Nagy, Andras; Duff, Kimberly; Bauer, Alexander; Okonneh, Fred; Rondon, Juan Carlos; Yel, Leman; Li, Zhaoyang

Postauthorization safety surveillance study of antihaemophilic factor (recombinant) reconstituted in 2 mL sterile water for injection in children with haemophilia A

抗血友病因子(重组)溶于2 mL注射用无菌水中,用于治疗A型血友病患儿的上市后安全性监测研究

Motwani, Jayashree; Guillet, Benoit; Blatny, Jan; Schilling, Freimut H; Wibaut, Bénédicte; Goldstine, Jimena; Nagy, Andras; Doralt, Jennifer; Engl, Werner; Tangada, Srilatha; Spotts, Gerald

Transcription factor ASCL2 is required for development of the glycogen trophoblast cell lineage.

转录因子 ASCL2 是糖原滋养层细胞谱系发育所必需的

Bogutz Aaron B, Oh-McGinnis Rosemary, Jacob Karen J, Ho-Lau Rita, Gu Ting, Gertsenstein Marina, Nagy Andras, Lefebvre Louis