日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNA editing for the treatment of alpha-1 antitrypsin deficiency.

RNA 编辑用于治疗 α-1 抗胰蛋白酶缺乏症。

Monian Prashant, Shivalila Chikdu, Lu Genliang, Bowman Keith, Briem Stearne, Bylsma Marissa, Byrne Michael, Cannon Megan, Chatterjee Arindom, Dallaire Morgan, Desai Jigar, Dufresne Jason, Faraone Alyse, Favaloro Frank, Friend Stephen, Ghosh Anamitra, Godfrey Jack, Hernandez Nidia, Huth Olivia, Iwamoto Naoki, Kawamoto Tomomi, Lamattina Anthony, Lemaitre Muriel, Lindsey Amber, Liu Fangjun, Looby Richard, Luu Khoa, McGlynn Andrew, Metterville Jake, Paik Ik-Hyeon, Pan Qianli, Patil Saurabh, Pu Tom, Purcell-Estabrook Erin, Ranade Ashwini, Rheinhardt Jeanette, Rossi Jeff, Shimizu Mamoru, Singh Kuldeep, Standley Stephany, Thomas Carina, Tripathi Snehlata, Yang Hailin, Yordanoff Ryan, Yin Yuan, Yu Hui, Narayanan PadmaKumar, Kandasamy Pachamuthu, Giangrande Paloma H, Vargeese Chandra

Cellular immune changes during severe antisense oligonucleotide-associated thrombocytopenia in a nonhuman primate model

非人灵长类动物模型中严重反义寡核苷酸相关血小板减少症期间的细胞免疫变化

Gupta, Sheena; Shen, Lijiang; Henry, Scott P; Aghaeepour, Nima; Narayanan, Padmakumar; Maecker, Holden T

Sequence-specific 2'-O-methoxyethyl antisense oligonucleotides activate human platelets through glycoprotein VI, triggering formation of platelet-leukocyte aggregates

序列特异性2'-O-甲氧基乙基反义寡核苷酸通过糖蛋白VI激活人血小板,触发血小板-白细胞聚集体的形成。

Slingsby, Martina H Lundberg; Vijey, Prakrith; Tsai, I-Ting; Roweth, Harvey; Couldwell, Genevieve; Wilkie, Adrian R; Gaus, Hans; Goolsby, Jazana M; Okazaki, Ross; Terkovich, Brooke E; Semple, John W; Thon, Jonathan N; Henry, Scott P; Narayanan, Padmakumar; Italiano, Joseph E Jr