Effectiveness and safety of everolimus treatment in patients with tuberous sclerosis complex in real-world clinical practice
依维莫司治疗结节性硬化症患者在真实世界临床实践中的有效性和安全性
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-023-02982-1
Cockerell, Ine; Christensen, Jakob; Hoei-Hansen, Christina E; Holst, Lotte; Grenaa Frederiksen, Mikkel; Issa-Epe, Aart Imran; Nedregaard, Bård; Solhoff, Ragnar; Heimdal, Ketil; Johannessen Landmark, Cecilie; Lund, Caroline; Nærland, Terje