Pharmacological and pre-clinical safety profile of rSIV.F/HN, a hybrid lentiviral vector for cystic fibrosis gene therapy
rSIV.F/HN(一种用于囊性纤维化基因治疗的混合慢病毒载体)的药理学和临床前安全性概况
期刊:European Respiratory Journal
影响因子:21
doi:10.1183/13993003.01683-2023
Moiseenko, Alena; Sinadinos, Anthony; Sergijenko, Ana; Pineault, Kyriel; Saleh, Aarash; Nekola, Konradin; Strang, Nathalie; Eleftheraki, Anastasia; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Hyde, Stephen C; McLachlan, Gerry; Rath, Tim; Rothe, Michael; Schambach, Axel; Hobbie, Silke; Schuler, Michael; Maier, Udo; Thomas, Matthew J; Mennerich, Detlev; Schmidt, Manfred; Griesenbach, Uta; Alton, Eric W F W; Kreuz, Sebastian