日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

An siRNA targeting S6k1 identifies photoreceptor phospholipid metabolism as a contributor to lipid buildup in age-related macular degeneration.

针对 S6k1 的 siRNA 发现光感受器磷脂代谢是导致年龄相关性黄斑变性中脂质积累的因素之一。

Cheng Shun-Yun, Giguere Delaney, Kim San, Seddon Johanna M, Caiazzi Jillian, Gross Katherine, McHugh Nicholas, Echeverria Dimas, Alterman Julia F, Gray-Edwards Heather, Benatti Hector Ribeiro, Renner Lauren, Woolard Hannah, Stoddard Jonathan, McGill Trevor J, Neuringer Martha, Brush Richard S, Agbaga Martin-Paul, Khvorova Anastasia, Punzo Claudio

Analysis of Cytosine Base Editors in Bovine Zygotes: Efficiency and Editing Window Characterization Through Targeting the MYO7A Gene

牛合子胞嘧啶碱基编辑器的分析:通过靶向 MYO7A 基因进行效率和编辑窗口表征

Ryu, Junghyun; Tippner-Hedges, Rebecca; Neuringer, Martha; Hennebold, Jon D

Preformed Vesicle Approach to LNP Manufacturing Enhances Retinal mRNA Delivery.

预成型囊泡法制备LNP可增强视网膜mRNA递送

Eygeris Yulia, Henderson Michael I, Curtis Allison G, Jozić Antony, Stoddard Jonathan, Reynaga Rene, Chirco Kathleen R, Su Grace Li-Na, Neuringer Martha, Lauer Andreas K, Ryals Renee C, Sahay Gaurav

Thiophene-based lipids for mRNA delivery to pulmonary and retinal tissues

基于噻吩的脂质体用于将mRNA递送至肺部和视网膜组织

Eygeris, Yulia; Gupta, Mohit; Kim, Jeonghwan; Jozic, Antony; Gautam, Milan; Renner, Jonas; Nelson, Dylan; Bloom, Elissa; Tuttle, Adam; Stoddard, Jonathan; Reynaga, Rene; Neuringer, Martha; Lauer, Andreas K; Ryals, Renee C; Sahay, Gaurav

Wide-field OCT angiography for non-human primate retinal imaging

用于非人灵长类动物视网膜成像的广角OCT血管造影

Wei, Xiang; Hormel, Tristan T; Renner, Laurie; Neuringer, Martha; Jia, Yali

Development of a translatable gene augmentation therapy for CNGB1-retinitis pigmentosa

开发一种可转化的基因增强疗法用于治疗 CNGB1 基因突变引起的视网膜色素变性

Occelli, Laurence M; Zobel, Lena; Stoddard, Jonathan; Wagner, Johanna; Pasmanter, Nathaniel; Querubin, Janice; Renner, Lauren M; Reynaga, Rene; Winkler, Paige A; Sun, Kelian; Marinho, Luis Felipe L P; O'Riordan, Catherine R; Frederick, Amy; Lauer, Andreas; Tsang, Stephen H; Hauswirth, William W; McGill, Trevor J; Neuringer, Martha; Michalakis, Stylianos; Petersen-Jones, Simon M

Early-in-life isoflurane exposure alters resting-state functional connectivity in juvenile non-human primates

幼年时期接触异氟烷会改变幼年非人灵长类动物的静息态功能连接。

Neudecker, Viola; Perez-Zoghbi, Jose F; Miranda-Domínguez, Oscar; Schenning, Katie J; Ramirez, Julian Sb; Mitchell, A J; Perrone, Anders; Earl, Eric; Carpenter, Sam; Martin, Lauren D; Coleman, Kristine; Neuringer, Martha; Kroenke, Christopher D; Dissen, Gregory A; Fair, Damien A; Brambrink, Ansgar M

Genetic variants in melanogenesis proteins TYRP1 and TYR are associated with the golden rhesus macaque phenotype

黑色素生成蛋白TYRP1和TYR的遗传变异与金丝猴表型相关

Peterson, Samuel M; Watowich, Marina M; Renner, Lauren M; Martin, Samantha; Offenberg, Emma; Lea, Amanda; Montague, Michael J; Higham, James P; Snyder-Mackler, Noah; Neuringer, Martha; Ferguson, Betsy

CRISPR/Cas9 editing of the MYO7A gene in rhesus macaque embryos to generate a primate model of Usher syndrome type 1B

利用 CRISPR/Cas9 技术编辑恒河猴胚胎中的 MYO7A 基因,构建 Usher 综合征 1B 型灵长类动物模型

Ryu, Junghyun; Statz, John P; Chan, William; Burch, Fernanda C; Brigande, John V; Kempton, Beth; Porsov, Edward V; Renner, Lauren; McGill, Trevor; Burwitz, Benjamin J; Hanna, Carol B; Neuringer, Martha; Hennebold, Jon D

Carotenoids improve the development of cerebral cortical networks in formula-fed infant macaques

类胡萝卜素可改善配方奶喂养的幼年猕猴大脑皮层网络的发育

Miranda-Dominguez, Oscar; Ramirez, Julian S B; Mitchell, A J; Perrone, Anders; Earl, Eric; Carpenter, Sam; Feczko, Eric; Graham, Alice; Jeon, Sookyoung; Cohen, Neal J; Renner, Laurie; Neuringer, Martha; Kuchan, Matthew J; Erdman, John W Jr; Fair, Damien