Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy
在接受视网膜下基因治疗的X连锁视网膜色素变性犬模型中,使用两种RPGR转基因进行剂量范围探索研究
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2019.337
Song, Chunjuan; Dufour, Valérie L; Cideciyan, Artur V; Ye, Guo-Jie; Swider, Malgorzata; Newmark, Judith A; Timmers, Adrian M; Robinson, Paulette M; Knop, David R; Chulay, Jeffrey D; Jacobson, Samuel G; Aguirre, Gustavo D; Beltran, William A; Shearman, Mark S