Neurocognitive assessment platform for clinical trials in PKU: White paper developed by the NPKUA neurocognitive workgroup
苯丙酮尿症临床试验的神经认知评估平台:NPKUA神经认知工作组编写的白皮书
期刊:Molecular Genetics and Metabolism
影响因子:3.5
doi:10.1016/j.ymgme.2024.108555
Waisbren, Susan E; Christ, Shawn E; Bilder, Deborah A; Bjoraker, Kendra J; Bolton, Scout; Chamberlin, Sarah; Grant, Mitzie L; Janzen, Darren M; Katz, Rachel; Lubliner, Eugene; Martin, Arianna; McQueen, Kelsey; Moshkovich, Olga; Nguyen-Driver, Mina; Shim, Soo; Stefanatos, Arianna K; Wilkening, Greta; Harding, Cary