Modified Polycyclic Compounds Rescue Mis-splicing in Myotonic Dystrophy Type 1 Disease Models.
修饰的多环化合物可挽救 1 型强直性肌营养不良症疾病模型中的错误剪接。
期刊:ACS Chemical Biology
影响因子:3.8
doi:10.1021/acschembio.5c00790
Frias Jesus A, Hicks Sawyer M, Mazdiyasni Hormoz, Mishra Subodh K, Sarkar Kahini, Yeboah Clara, LeFever Noah M, Scotti Marina M, Zeghal Hana, Brandt Naomi, Vangaveti Sweta, Chakma Pramita, Wang Ting, Reid Tammy S, McMichael Omari, Crumbaugh Christopher, Provenzano Marina, Hale Melissa A, Cleary John D, Johnson Nicholas E, Wang Eric T, Reddy Kaalak, Berglund J Andrew