Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo
自我递送、化学修饰的 CRISPR RNA,用于 AAV 共递送和体内基因组编辑
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gkad1125
Han Zhang, Karen Kelly, Jonathan Lee, Dimas Echeverria, David Cooper, Rebecca Panwala, Nadia Amrani, Zexiang Chen, Nicholas Gaston, Atish Wagh, Gregory A Newby, Jun Xie, David R Liu, Guangping Gao, Scot A Wolfe, Anastasia Khvorova, Jonathan K Watts, Erik J Sontheimer