日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo

自我递送、化学修饰的 CRISPR RNA,用于 AAV 共递送和体内基因组编辑

Han Zhang, Karen Kelly, Jonathan Lee, Dimas Echeverria, David Cooper, Rebecca Panwala, Nadia Amrani, Zexiang Chen, Nicholas Gaston, Atish Wagh, Gregory A Newby, Jun Xie, David R Liu, Guangping Gao, Scot A Wolfe, Anastasia Khvorova, Jonathan K Watts, Erik J Sontheimer

Domain-inlaid Nme2Cas9 adenine base editors with improved activity and targeting scope

具有改进的活性和靶向范围的域镶嵌 Nme2Cas9 腺嘌呤碱基编辑器

Nathan Bamidele, Han Zhang, Xiaolong Dong, Haoyang Cheng, Nicholas Gaston, Hailey Feinzig, Hanbing Cao, Karen Kelly, Jonathan K Watts, Jun Xie, Guangping Gao, Erik J Sontheimer

A Fluorescent Reporter Mouse for In Vivo Assessment of Genome Editing with Diverse Cas Nucleases and Prime Editors

一种用于体内评估多种Cas核酸酶和Prime编辑器基因组编辑的荧光报告小鼠

Zexiang Chen ,Suet-Yan Kwan ,Aamir Mir ,Max Hazeltine ,Minwook Shin ,Shun-Qing Liang ,Io Long Chan ,Karen Kelly ,Krishna S Ghanta ,Nicholas Gaston ,Yueying Cao ,Jun Xie ,Guangping Gao ,Wen Xue ,Erik J Sontheimer ,Jonathan K Watts

Self-delivering CRISPR RNAs for AAV Co-delivery and Genome Editing in vivo

用于 AAV 共递送和体内基因组编辑的自递送 CRISPR RNA

Han Zhang, Karen Kelly, Jonathan Lee, Dimas Echeverria, David Cooper, Rebecca Panwala, Zexiang Chen, Nicholas Gaston, Gregory A Newby, Jun Xie, David R Liu, Guangping Gao, Scot A Wolfe, Anastasia Khvorova, Jonathan K Watts, Erik J Sontheimer

Engineering Nme2Cas9 Adenine Base Editors with Improved Activity and Targeting Scope

工程化 Nme2Cas9 腺嘌呤碱基编辑器,提高活性和靶向范围

Nathan Bamidele, Han Zhang, Xiaolong Dong, Nicholas Gaston, Haoyang Cheng, Karen Kelly, Jonathan K Watts, Jun Xie, Guangping Gao, Erik J Sontheimer