A pothole-filling strategy for selective targeting of rCUG-repeats associated with myotonic dystrophy type 1
一种针对与1型强直性肌营养不良症相关的rCUG重复序列的选择性靶向治疗策略
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.2507065123
Perera, J Dinithi R; Thadke, Shivaji A; Thrikawala, Savani W; Dhami, Isha; Hridya, V M; Mukherjee, Arnab; Paul, Ananya; Wilson, W David; Tan, Keith W R; Chan, Nicholas Z W; Phan, Anh Tuân; Ly, Danith H
