日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Treatment of canine hemophilia A via intraosseous delivery of a platelet-specific factor VIII-lentiviral vector

通过骨内注射血小板特异性因子VIII慢病毒载体治疗犬血友病A

Rementer, Cameron W; Li, Chong; Nichols, Timothy C; Cai, Xiaohe; Joo, Julia; Wang, Xuefeng; Kloos, Mark; George, Nneka; Chao, Ting-Yen; Xu, Yuanyi; Poncz, Mortimer; Ochs, Hans D; Rawlings, David J; Miao, Carol H

AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life

针对患有严重血友病的伴侣犬的AAV基因疗法:关于免疫原性、疗效和生活质量的真实世界长期数据

Doshi, Bhavya S; Samelson-Jones, Benjamin J; Nichols, Timothy C; Merricks, Elizabeth P; Siner, Joshua L; French, Robert A; Lee, Ben J; Arruda, Valder R; Callan, Mary Beth

Recombinant von Willebrand factor and tranexamic acid for heavy menstrual bleeding in patients with mild and moderate von Willebrand disease in the USA (VWDMin): a phase 3, open-label, randomised, crossover trial

在美国,一项针对轻度至中度血管性血友病(VWDMin)患者,采用重组血管性血友病因子和氨甲环酸治疗月经过多的3期开放标签随机交叉试验

Ragni, Margaret V; Rothenberger, Scott D; Feldman, Robert; Nance, Danielle; Leavitt, Andrew D; Malec, Lynn; Kulkarni, Roshni; Sidonio, Robert Jr; Kraut, Eric; Lasky, Joseph; Pruthi, Rajiv; Angelini, Dana; Philipp, Claire; Hwang, Nina; Wheeler, Allison P; Seaman, Craig; Machin, Nicoletta; Xavier, Frederico; Meyer, Michael; Bellissimo, Daniel; Humphreys, Gregory; Smith, Kenneth J; Merricks, Elizabeth P; Nichols, Timothy C; Ivanco, Dana; Vehec, Deborah; Koerbel, Glory; Althouse, Andrew D

Mechanisms of Foreign Body Response Mitigation by Nitric Oxide Release

一氧化氮释放缓解异物反应的机制

Taylor, James B; Malone-Povolny, Maggie J; Merricks, Elizabeth P; Wimsey, Lauren E; Soliman, Daniel; Nichols, Timothy C; Wallet, Shannon M; Maile, Robert; Schoenfisch, Mark H

Adeno-associated virus-mediated expression of activated factor V (FVa) for hemophilia phenotypic correction

腺相关病毒介导的活化因子V(FVa)表达用于血友病表型矫正

Sun, Junjiang; Chen, Xiaojing; Chai, Zheng; Niu, Hongqian; Dobbins, Amanda L; Nichols, Timothy C; Li, Chengwen

Evolutionary insights into coagulation factor IX Padua and other high-specific-activity variants

对凝血因子IX Padua和其他高比活性变体的进化见解

Samelson-Jones, Benjamin J; Finn, Jonathan D; Raffini, Leslie J; Merricks, Elizabeth P; Camire, Rodney M; Nichols, Timothy C; Arruda, Valder R

Preclinical evaluation of a next-generation, subcutaneously administered, coagulation factor IX variant, dalcinonacog alfa

对新一代皮下注射凝血因子IX变体dalcinonacog alfa进行临床前评估

Nichols, Timothy C; Levy, Howard; Merricks, Elizabeth P; Raymer, Robin A; Lee, Martin L

Long-Term Accurate Continuous Glucose Biosensors via Extended Nitric Oxide Release

通过延长一氧化氮释放实现长期、精确的连续葡萄糖生物传感器

Malone-Povolny, Maggie J; Merricks, Elizabeth P; Wimsey, Lauren E; Nichols, Timothy C; Schoenfisch, Mark H

Delineation of Human Carotid Plaque Features In Vivo by Exploiting Displacement Variance

利用位移方差在体内描绘人类颈动脉斑块特征

Torres, Gabriela; Czernuszewicz, Tomasz J; Homeister, Jonathon W; Caughey, Melissa C; Huang, Benjamin Y; Lee, Ellie R; Zamora, Carlos A; Farber, Mark A; Marston, William A; Huang, David Y; Nichols, Timothy C; Gallippi, Caterina M

Mechanical Anisotropy Assessment in Kidney Cortex Using ARFI Peak Displacement: Preclinical Validation and Pilot In Vivo Clinical Results in Kidney Allografts

利用ARFI峰值位移评估肾皮质的力学各向异性:肾移植的临床前验证和初步体内临床试验结果

Hossain, Md Murad; Detwiler, Randal K; Chang, Emily H; Caughey, Melissa C; Fisher, Melrose W; Nichols, Timothy C; Merricks, Elizabeth P; Raymer, Robin A; Whitford, Margaret; Bellinger, Dwight A; Wimsey, Lauren E; Gallippi, Caterina M