Development of an adeno-associated virus vector for gene replacement therapy of NF1-related tumors
开发用于NF1相关肿瘤基因替代疗法的腺相关病毒载体
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-025-63619-4.
Ren-Yuan Bai ,Jingyi Shi ,Jianan Liu ,Nihao Sun ,Yuqing Lu ,Xiaojun Chen ,Manzhu Xu ,Hotae Lim ,Yang Li ,Huazhen Xu ,Karis Weisgerber ,Zhihong Ren ,Christine A Pratilas ,Jaishri O Blakeley ,Melissa L Fishel ,Meritxell Carrió ,Eduard Serra ,Verena Staedtke